Toxicity of cationic lipids and cationic polymers in gene delivery
Tài liệu tham khảo
El-Aneed, 2004, An overview of current delivery systems in cancer gene therapy, J. Control. Release, 94, 1, 10.1016/j.jconrel.2003.09.013
Rolland, 2005, Gene medicines: the end of the beginning?, Adv. Drug Deliv. Rev., 57, 669, 10.1016/j.addr.2005.01.002
Cusack, 2002, Introduction to cancer gene therapy, Surg. Oncol. Clin. N. Am., 11, 497, 10.1016/S1055-3207(02)00029-7
Senior, 1991, Interaction of positively-charged liposomes with blood: implications for their application in vivo, Biochim. Biophys. Acta, 1070, 173, 10.1016/0005-2736(91)90160-A
Sakurai, 2001, Interaction between DNA-cationic liposome complexes and erythrocytes is an important factor in systemic gene transfer via the intravenous route in mice: the role of the neutral helper lipid, Gene Ther., 8, 677, 10.1038/sj.gt.3301460
Jahnova, 1994, Amphiphilic detergents inhibit production of IgG and IgM by human peripheral blood mononuclear cells, Immunol. Lett., 39, 71, 10.1016/0165-2478(93)90166-Y
Filion, 1997, Toxicity and immunomodulatory activity of some liposomal vectors formulated with cationic lipids toward immune effector cells, Biochim. Biophys. Acta, 1329, 345, 10.1016/S0005-2736(97)00126-0
Derelanko, 2002
Lappalainen, 1994, Comparison of cell proliferation and toxicity assays using two cationic liposomes, Pharm. Res., 11, 1127, 10.1023/A:1018932714745
Aberle, 1998, A novel tetraester construct that reduces cationic lipid-associated cytotoxicity. Implications for the onset of cytotoxicity, Biochemistry, 37, 6533, 10.1021/bi9801154
Felgner, 1987, Lipofection: a highly efficient, lipid-mediated DNA-transfection procedure, Proc. Natl. Acad. Sci., 84, 7413, 10.1073/pnas.84.21.7413
Gao, 2001, Synthesis of a novel series of cationic lipids that can act as efficient gene delivery vehicles through systematic heterocyclic substitution of cholesterol derivatives, Gene Ther., 8, 855, 10.1038/sj.gt.3301471
Pinnaduwage, 1989, Use of a quaternary ammonium detergent in liposome mediated DNA transfection of mouse L-cells, Biochim. Biophys. Acta, 985, 33, 10.1016/0005-2736(89)90099-0
Tang, 1999, Synthesis of a single-tailed cationic lipid and investigation of its transfection, J. Control. Release, 62, 345, 10.1016/S0168-3659(99)00158-3
Bottega, 1992, Inhibition of protein kinase C by cationic amphiphiles, Biochemistry, 31, 9025, 10.1021/bi00152a045
Kawakami, 1998, Asialoglycoprotein receptor-mediated gene transfer using novel galactosylated cationic liposomes, Biochem. Biophys. Res.Commun., 252, 78, 10.1006/bbrc.1998.9602
Floch, 2000, Cation substitution in cationic phosphonolipids: a new concept to improve transfection activity and decrease cellular toxicity, J. Med. Chem., 30, 4617, 10.1021/jm000006z
Heyes, 2002, Synthesis of novel cationic lipids: effect of structural modification on the efficiency of gene transfer, J. Med. Chem., 45, 99, 10.1021/jm010918g
Solodin, 1995, A novel series of amphiphilic imidazolinium compounds for in vitro and in vivo gene delivery, Biochemistry, 34, 13537, 10.1021/bi00041a033
van der Woude, 1997, Novel pyridinium surfactants for efficient, nontoxic in vitro gene delivery, Proc. Natl. Acad. Sci. U. S. A., 94, 1160, 10.1073/pnas.94.4.1160
Meekel, 2000, Synthesis of pyridinium amphiphiles used for transfection and some characteristics of amphiphile/DNA complex formation, Eur. J. Org. Chem., 4, 665, 10.1002/(SICI)1099-0690(200002)2000:4<665::AID-EJOC665>3.0.CO;2-A
Roosjen, 2002, Synthesis and characteristics of biodegradable pyridinium amphiphiles used for in vitro DNA delivery, Eur. J. Org. Chem., 7, 1271, 10.1002/1099-0690(200204)2002:7<1271::AID-EJOC1271>3.0.CO;2-G
Ilies, 2003, Pyridinium-based cationic lipids as gene-transfer agents, Eur. J. Org. Chem., 14, 2645, 10.1002/ejoc.200300106
Yingyongnarongkul, 2004, Solid-phase synthesis of 89 polyamine-based cationic lipids for DNA delivery to mammalian cells, Chem. Eur. J., 10, 463, 10.1002/chem.200305232
Freedland, 1996, Toxicity of cationic lipid-ribozyme complexes in human prostate tumor cells can mimic ribozyme activity, Biochem. Mol. Med., 59, 144, 10.1006/bmme.1996.0080
Leventis, 1990, Interactions of mammalian cells with lipid dispersions containing novel metabolizable cationic amphiphiles, Biochim. Biophys. Acta, 1023, 124, 10.1016/0005-2736(90)90017-I
Choi, 2001, New cationic liposomes for gene transfer into mammalian cells with high efficiency and low toxicity, Bioconjug. Chem., 12, 108, 10.1021/bc000081o
Liu, 2005, Synthesis of carbamate-linked lipids for gene delivery, Bioorg. Med. Chem. Lett., 15, 3147, 10.1016/j.bmcl.2005.04.010
Boomer, 1999, Synthesis of acid-labile diplasmenyl lipids for drug and gene delivery applications, Chem. Phys. Lipids, 99, 145, 10.1016/S0009-3084(99)00033-X
Boomer, 2002, Formation of plasmid-based transfection complexes with an acid-labile cationic lipid: characterization of in vitro and in vivo gene transfer, Pharm. Res., 19, 1292, 10.1023/A:1020342523694
Mirska, 2005, Biophysical and biochemical properties of a binary lipid mixture for DNA transfection, Colloids Surf., B Biointerfaces, 40, 51, 10.1016/j.colsurfb.2004.10.007
Li, 1998, Characterization of cationic lipid-protamine-DNA (LPD) complexes for intravenous gene delivery, Gene Ther., 5, 930, 10.1038/sj.gt.3300683
Friend, 1996, Endocytosis and intracellular processing accompanying transfection mediated by cationic liposomes, Biochim. Biophys. Acta, 1278, 41, 10.1016/0005-2736(95)00219-7
Dass, 2002, Vehicles for oligonucleotide delivery: therapeutic applicability against tumors, J. Pharm. Pharmacol., 54, 3, 10.1211/0022357021771887
Felgner, 1994, Enhanced gene delivery and mechanism studies with a novel series of cationic lipid formulations, J. Biol. Chem., 269, 2550, 10.1016/S0021-9258(17)41980-6
Hafez, 2001, On the mechanism whereby cationic lipids promote intracellular delivery of polynucleic acids, Gene Ther., 8, 1188, 10.1038/sj.gt.3301506
Tempelton, 1997, Improved DNA: liposomes complexes for increased systemic delivery and gene expression, Nat. Biotechnol., 15, 647, 10.1038/nbt0797-647
Tokunaga, 2004, Effect of oligopeptides on gene expression: comparison of DNA/peptide and DNA/peptide/liposome complexes, Int. J. Pharm., 269, 71, 10.1016/j.ijpharm.2003.08.018
Lasic, 1997
Gershon, 1993, Mode of formation and structural features of DNA-cationic liposome complexes used for transfection, Biochemistry, 32, 7143, 10.1021/bi00079a011
Boussif, 1995, A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo: polyethylenimine, Proc. Natl. Acad. Sci., 92, 7297, 10.1073/pnas.92.16.7297
Kunath, 2003, Low-molecular-weight polyethylenimine as a non-viral vector for DNA delivery: comparison of physicochemical properties, transfection efficiency and in vivo distribution with high-molecular-weight polyethylenimine, J. Control. Release, 89, 113, 10.1016/S0168-3659(03)00076-2
Kircheis, 1999, Polycation-based DNA complexes for tumor-targeted gene delivery in vivo, J. Gene Med., 1, 111, 10.1002/(SICI)1521-2254(199903/04)1:2<111::AID-JGM22>3.0.CO;2-Y
Fischer, 1999, A novel non-viral vector for DNA delivery based on low molecular weight, branched polyethylenimine: effect of molecular weight on transfection efficiency and cytotoxicity, Pharm. Res., 16, 1273, 10.1023/A:1014861900478
Godbey, 1999, Size matters: molecular weight affects the efficiency of poly(ethylenimine) as a gene delivery vehicle, J. Biomed. Mater. Res., 45, 268, 10.1002/(SICI)1097-4636(19990605)45:3<268::AID-JBM15>3.0.CO;2-Q
Godbey, 1999, Improved packing of poly(ethyleneimine)/DNA complexes increases transfection efficiency, Gene Ther., 6, 1380, 10.1038/sj.gt.3300976
Petersen, 2002, Poly(ethylenimine-co-l-lactamide-co-succinamide): a biodegradable polyethylenimine derivative with an advantageous pH-dependent hydrolytic degradation for gene delivery, Bioconjug. Chem., 13, 812, 10.1021/bc0255135
Petersen, 2002, Polyethylenimine-graft-poly(ethylene glycol) copolymers: influence of copolymer block structure on DNA complexation and biological activities as gene delivery system, Bioconjug. Chem., 13, 845, 10.1021/bc025529v
Thomas, 2005, Full deacylation of polyethylenimine dramatically boosts its gene delivery efficiency and specificity to mouse lung, Proc. Natl. Acad. Sci., 102, 5679, 10.1073/pnas.0502067102
Tang, 2006, Low molecular weight polyethylenimines linked by beta-cyclodextrin for gene transfer into the nervous system, J. Gene Med., 8, 736, 10.1002/jgm.874
Han, 2001, Water-soluble lipopolymer for gene delivery, Bioconjug. Chem., 12, 337, 10.1021/bc000120w
Wang, 2002, Novel branched poly(ethylenimine)–cholesterol water-soluble lipopolymers for gene delivery, Biomacromolecules, 3, 1197, 10.1021/bm025563c
Mahato, 2005, Water insoluble and soluble lipids for gene delivery, Adv. Drug Deliv. Rev., 57, 699, 10.1016/j.addr.2004.12.005
Pannier, 2004, Controlled release systems for DNA delivery, Mol. Ther., 10, 19, 10.1016/j.ymthe.2004.03.020
Kneuer, 2000, A nonviral DNA delivery system based on surface modified silica-nanoparticles can efficiently transfect cells in vitro, Bioconjug. Chem., 11, 926, 10.1021/bc0000637
Manuel, 2001, Transfection by polyethyleneimine-coated microspheres, J. Drug Target., 9, 15, 10.3109/10611860108995629
Ward, 2001, Systemic circulation of poly(l-lysine)/DNA vectors is influenced by polycation molecular weight and type of DNA: differential circulation in mice and rats and the implications for human gene therapy, Blood, 97, 2221, 10.1182/blood.V97.8.2221
Pouton, 1998, Polycation-DNA complexes for gene delivery: a comparison of the biopharmaceutical properties of cationic polypeptides and cationic lipids, J. Control. Release, 53, 289, 10.1016/S0168-3659(98)00015-7
Shewring, 1997, A nonviral vector system for efficient gene transfer to corneal endothelial cells via membrane integrins, Transplantation, 64, 763, 10.1097/00007890-199709150-00018
Funhoff, 2005, Cationic polymethacrylates with covalently linked membrane destabilizing peptides as gene delivery vectors, J. Control. Release, 101, 233, 10.1016/j.jconrel.2004.06.023
Ward, 2002, Modification of pLL/DNA complexes with a multivalent hydrophilic polymer permits folate-mediated targeting in vitro and prolonged plasma circulation in vivo, J. Gene Med., 4, 536, 10.1002/jgm.296
Wolfert, 1999, Polyelectrolyte vectors for gene delivery: influence of cationic polymer on biophysical properties of complexes formed with DNA, Bioconjug. Chem., 10, 993, 10.1021/bc990025r
Ohsaki, 2002, In vitro gene transfection using dendritic poly(l-lysine), Bioconjug. Chem., 13, 510, 10.1021/bc015525a
Okuda, 2004, Characters of dendritic poly(l-lysine) analogues with the terminal lysines replaced with arginines and histidines as gene carriers in vitro, Biomaterials, 25, 537, 10.1016/S0142-9612(03)00542-8
Brown, 2000, Preliminary characterization of novel amino acid based polymeric vesicles as gene and drug delivery agents, Bioconjug. Chem., 11, 880, 10.1021/bc000052d
Koping-Hoggard, 2003, Relationship between the physical shape and the efficiency of oligomeric chitosan as a gene delivery system in vitro and in vivo, J. Gene Med., 5, 130, 10.1002/jgm.327
Lee, 2001, Water-soluble and low molecular weight chitosan-based plasmid DNA delivery, Pharm. Res., 18, 427, 10.1023/A:1011037807261
Illum, 1994, Chitosan as a novel nasal system for peptide drugs, Pharm. Res., 11, 1186, 10.1023/A:1018901302450
Verhoef, 2001, Chitosan and its derivatives as intestinal absorption enhancers, Adv. Drug Deliv. Rev., 50, 91, 10.1016/S0169-409X(01)00180-6
Azzam, 2002, Cationic polysaccharides for gene delivery, Macromolecules, 35, 9947, 10.1021/ma0209592
Yudovin-Farber, 2005, Quaternary ammonium polysaccharides for gene delivery, Bioconjug. Chem., 16, 1196, 10.1021/bc050066p
Eliyahu, 2005, Novel dextran-spermine conjugates as transfecting agents: comparing water-soluble and micellar polymers, Gene Ther., 12, 494, 10.1038/sj.gt.3302395
Eliyahu, 2006, Dextran-spermine-based polyplexes—evaluation of transgene expression and of local and systemic toxicity in mice, Biomaterials, 27, 1636, 10.1016/j.biomaterials.2005.08.024
Vincent, 2003, Efficacy of dendrimer-mediated angiostatin and TIMP-2 gene delivery on inhibition of tumor growth and angiogenesis: in vitro and in vivo studies, Int. J. Cancer, 105, 419, 10.1002/ijc.11105
Funhoff, 2004, Endosomal escape of polymeric gene delivery complexes is not always enhanced by polymers buffering at low pH, Biomacromolecules, 5, 32, 10.1021/bm034041+
Read, 2003, Vectors based on reducible polycations facilitate intracellular release of nucleic acids, J. Gene Med., 5, 232, 10.1002/jgm.331
Maheshwari, 2002, Biodegradable polymer-based interleukin-12 gene delivery: role of induced cytokines, tumor infiltrating cells and nitric oxide in anti-tumor activity, Gene Ther., 9, 1075, 10.1038/sj.gt.3301766