Molecular Therapy - Methods & Clinical Development

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AAV6 Vexosomes Mediate Robust Suicide Gene Delivery in a Murine Model of Hepatocellular Carcinoma
Molecular Therapy - Methods & Clinical Development - Tập 17 - Trang 497-504 - 2020
Nusrat Khan, Shubham Maurya, Sridhar Bammidi, Giridhara R. Jayandharan
A universal protocol for isolating retinal ON bipolar cells across species via fluorescence-activated cell sorting
Molecular Therapy - Methods & Clinical Development - Tập 20 - Trang 587-600 - 2021
Elisa Murenu, Marina Pavlou, Lisa Richter, Kleopatra Rapti, Sabrina Just, Jasmina Cehajic-Kapetanovic, Neda Tafrishi, Andrew Hayes, Rachel Scholey, Robert Lucas, Hildegard Büning, Dirk Grimm, Stylianos Michalakis
Use of 27G needles improves sensitivity and performance of ATCC anaerobe reference microorganism detection in BacT/Alert system
Molecular Therapy - Methods & Clinical Development - Tập 20 - Trang 542-550 - 2021
Salvatore Pasqua, Giampiero Vitale, Anna Pasquariello, Bruno Douradinha, Fabio Tuzzolino, Francesca Cardinale, Chiara Cusimano, Chiara Di Bartolo, Pier Giulio Conaldi, Danilo D’Apolito
Surface-Engineered Lentiviral Vectors for Selective Gene Transfer into Subtypes of Lymphocytes
Molecular Therapy - Methods & Clinical Development - Tập 12 - Trang 19-31 - 2019
Annika M. Frank, Christian J. Buchholz
Targeted biallelic integration of an inducible Caspase 9 suicide gene in iPSCs for safer therapies
Molecular Therapy - Methods & Clinical Development - Tập 26 - Trang 84-94 - 2022
Stephanie Wunderlich, Alexandra Haase, Sylvia Merkert, Kirsten Jahn, Maximillian Deest, Helge Frieling, Silke Glage, Wilhelm Korte, Andreas Martens, Andreas Kirschning, Andre Zeug, Evgeni Ponimaskin, Gudrun Göhring, Mania Ackermann, Nico Lachmann, Thomas Moritz, Robert Zweigerdt, Ulrich Martin
A Direct Comparison of IV and ICV Delivery Methods for Gene Replacement Therapy in a Mouse Model of SMARD1
Molecular Therapy - Methods & Clinical Development - Tập 10 - Trang 348-360 - 2018
Monir Shababi, Eric Villalón, Kevin A. Kaifer, Vince DeMarco, Christian L. Lorson
The seroprevalence of neutralizing antibodies against the adeno-associated virus capsids in Japanese hemophiliacs
Molecular Therapy - Methods & Clinical Development - Tập 27 - Trang 404-414 - 2022
Yuji Kashiwakura, Nemekhbayar Baatartsogt, Shoji Yamazaki, Azusa Nagao, Kagehiro Amano, Nobuaki Suzuki, Tadashi Matsushita, Akihiro Sawada, Satoshi Higasa, Naoya Yamasaki, Teruhisa Fujii, Taemi Ogura, Hideyuki Takedani, Masashi Taki, Takeshi Matsumoto, Jun Yamanouchi, Michio Sakai, Masako Nishikawa, Yutaka Yatomi, Koji Yada
Development and characterization of an enhanced nonviral expression vector for electroporation cancer treatment
Molecular Therapy - Methods & Clinical Development - Tập 1 - Trang 14012 - 2014
Patrick F Forde, Lindsay J Hall, Mira Sadadcharam, Marcle de Kruijf, Gerald C O'Sullivan, Declan M Soden
Intrinsic Myogenic Potential of Skeletal Muscle-Derived Pericytes from Patients with Myotonic Dystrophy Type 1
Molecular Therapy - Methods & Clinical Development - Tập 15 - Trang 120-132 - 2019
Cornelia Rosanne Maria Ausems, Renée Henrica Lamberta Raaijmakers, Walterus Johannes Antonius Adriana van den Broek, Marieke Willemse, Baziel Gerardus Maria van Engelen, Derick Gert Wansink, Hans van Bokhoven
Purification of Human CD34+CD90+ HSCs Reduces Target Cell Population and Improves Lentiviral Transduction for Gene Therapy
Molecular Therapy - Methods & Clinical Development - Tập 18 - Trang 679-691 - 2020
Stefan Radtke, Dnyanada Pande, Margaret Cui, Anai M. Perez, Yan-Yi Chan, Mark Enstrom, Stefanie Schmuck, Andrew Berger, Tom Eunson, Jennifer E. Adair, Hans-Peter Kiem
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