A Direct Comparison of IV and ICV Delivery Methods for Gene Replacement Therapy in a Mouse Model of SMARD1

Molecular Therapy - Methods & Clinical Development - Tập 10 - Trang 348-360 - 2018
Monir Shababi1,2, Eric Villalón1,2, Kevin A. Kaifer1,2, Vince DeMarco3,4,5, Christian L. Lorson1,2
1Department of Veterinary Pathobiology, College of Veterinary Medicine, University of Missouri, Columbia, MO, USA
2Bond Life Sciences Center, University of Missouri, Columbia, MO, USA
3Department of Medicine, Division of Endocrinology, Diabetes and Cardiovascular Center, University of Missouri, Columbia, MO, USA
4Department of Medical Pharmacology and Physiology, School of Medicine, University of Missouri, Columbia, MO, USA
5Research Service, Harry S. Truman Memorial Veterans Hospital, University of Missouri, Columbia, MO, USA

Tài liệu tham khảo

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