Human Gene Therapy
1043-0342
1557-7422
Mỹ
Cơ quản chủ quản: Mary Ann Liebert Inc.
Lĩnh vực:
Molecular MedicineGeneticsMolecular Biology
Các bài báo tiêu biểu
Treatment of Leber Congenital Amaurosis Due to<i>RPE65</i>Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial
Tập 19 Số 10 - Trang 979-990 - 2008
Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV Vectors
Tập 21 Số 6 - Trang 704-712 - 2010
Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN
Tập 29 Số 3 - Trang 285-298 - 2018
Gene Therapy by Intramuscular Injection of Plasmid DNA: Studies on Firefly Luciferase Gene Expression in Mice
Tập 4 Số 4 - Trang 419-431 - 1993
Assessment of Recombinant Adenoviral Vectors for Hepatic Gene Therapy
Tập 4 Số 4 - Trang 403-409 - 1993
Self-Inactivating Lentiviral Vectors with Enhanced Transgene Expression as Potential Gene Transfer System in Parkinson's Disease
Tập 11 Số 1 - Trang 179-190 - 2000
A Novel Tumor-Specific Replication-Restricted Adenoviral Vector for Gene Therapy of Hepatocellular Carcinoma
Tập 10 Số 10 - Trang 1721-1733 - 1999
Dynein- and Microtubule-Mediated Translocation of Adenovirus Serotype 5 Occurs after Endosomal Lysis
Tập 11 Số 1 - Trang 151-165 - 2000
Basis of Pulmonary Toxicity Associated with Cationic Lipid-Mediated Gene Transfer to the Mammalian Lung
Tập 8 Số 6 - Trang 689-707 - 1997
Acute Toxicity After High-Dose Systemic Injection of Helper-Dependent Adenoviral Vectors into Nonhuman Primates
Tập 15 Số 1 - Trang 35-46 - 2004