Oligonucleotides conjugated with short chemically defined polyethylene glycol chains are efficient antisense agents

Bioorganic & Medicinal Chemistry Letters - Tập 24 - Trang 5758-5761 - 2014
Nasrin Shokrzadeh1, Anna-Maria Winkler1, Mehrdad Dirin1, Johannes Winkler1
1University of Vienna, Department of Pharmaceutical Chemistry, Althanstraße 14, 1090 Vienna, Austria

Tài liệu tham khảo

Parhofer, 2012, Core Evid., 7, 29, 10.2147/CE.S25239 Sjouke, 2013, Curr. Opin. Lipidol., 24, 301, 10.1097/MOL.0b013e328362dfd9 Cirak, 2011, Lancet, 378, 595, 10.1016/S0140-6736(11)60756-3 Winkler, 2013, Ther. Delivery, 4, 791, 10.4155/tde.13.47 Aliabadi, 2012, Biomaterials, 33, 2546, 10.1016/j.biomaterials.2011.11.079 Ling, 2013, Nat. Rev. Drug Disc., 12, 847, 10.1038/nrd4140 van Rooij, 2011, Circ. Res., 108, 219, 10.1161/CIRCRESAHA.110.227496 Jansson, 2012, Mol. Oncol., 6, 590, 10.1016/j.molonc.2012.09.006 Gebert, 2014, Nucleic Acids Res., 42, 609, 10.1093/nar/gkt852 Zhang, 2013, J. Controlled Release, 172, 962, 10.1016/j.jconrel.2013.09.015 Dirin, 2013, Expert Opin. Biol. Ther., 13, 875, 10.1517/14712598.2013.774366 Gaziova, 2014, Bioorg. Med. Chem., 22, 2320, 10.1016/j.bmc.2014.02.004 Iversen, 2013, Theranostics, 3, 201, 10.7150/thno.5743 Stein, 2010, Nucleic Acids Res., 38, e3, 10.1093/nar/gkp841 Winkler, 2010, ChemMedChem, 5, 1344, 10.1002/cmdc.201000156 Winkler, 2008, ChemMedChem, 3, 102, 10.1002/cmdc.200700169 Astorgues-Xerri, 2014, Cancer Treat. Rev., 40, 307, 10.1016/j.ctrv.2013.07.007 Jost, 1992, J. Immunol. Methods, 147, 153, 10.1016/S0022-1759(12)80003-2