Mitochondrial drug delivery and mitochondrial disease therapy – An approach to liposome-based delivery targeted to mitochondria
Tài liệu tham khảo
Asoh, 2000, The super anti-apoptotic factor Bcl-xFNK constructed by disturbing intramolecular polar interactions in rat Bcl-xL, J. Biol. Chem., 275, 37240, 10.1074/jbc.M005841200
Asoh, 2002, Protection against ischemic brain injury by protein therapeutics, Proc. Natl. Acad. Sci. USA, 99, 17107, 10.1073/pnas.262460299
Asoh, 2005, Zonal necrosis prevented by transduction of the artificial anti-death FNK protein, Cell Death Differ., 12, 384, 10.1038/sj.cdd.4401569
D’Souza, 2005, Mitochondrial leader sequence-plasmid DNA conjugates delivered into mammalian cells by DQAsomes co-localize with mitochondria, Mitochondrion, 5, 352, 10.1016/j.mito.2005.07.001
Del Gaizo, 2003, A novel TAT-mitochondrial signal sequence fusion protein is processed, stays in mitochondria, and crosses the placenta, Mol. Ther., 7, 720, 10.1016/S1525-0016(03)00130-8
Embury, 2001, Proteins linked to a protein transduction domain efficiently transduce pancreatic islets, Diabetes, 50, 1706, 10.2337/diabetes.50.8.1706
Endo, 1995, Avidin fusion protein as a tool to generate a stable translocation intermediate spanning the mitochondrial membranes, J. Biochem. (Tokyo), 118, 753, 10.1093/oxfordjournals.jbchem.a124976
Goto, 1990, A mutation in the tRNA(Leu)(UUR) gene associated with the MELAS subgroup of mitochondrial encephalomyopathies, Nature, 348, 651, 10.1038/348651a0
Gupta, 2005, Intracellular delivery of large molecules and small particles by cell-penetrating proteins and peptides, Adv. Drug Deliv. Rev., 57, 637, 10.1016/j.addr.2004.10.007
Holt, 1988, Deletions of muscle mitochondrial DNA in patients with mitochondrial myopathies, Nature, 331, 717, 10.1038/331717a0
Kakudo, 2004, Transferrin-modified liposomes equipped with a pH-sensitive fusogenic peptide: an artificial viral-like delivery system, Biochemistry, 43, 5618, 10.1021/bi035802w
Kamiya, 2003, Pharmacokinetic and pharmacodynamic considerations in gene therapy, Drug Discov. Today, 8, 990, 10.1016/S1359-6446(03)02889-7
Khalil, 2006, High density of octaarginine stimulates macropinocytosis leading to efficient intracellular trafficking for gene expression, J. Biol. Chem., 281, 3544, 10.1074/jbc.M503202200
Mayer, 1995, Mitochondrial protein import: reversible binding of the presequence at the trans side of the outer membrane drives partial translocation and unfolding, Cell, 80, 127, 10.1016/0092-8674(95)90457-3
Moriguchi, 2005, A multifunctional envelope-type nano device for novel gene delivery of siRNA plasmids, Int. J. Pharm., 301, 277, 10.1016/j.ijpharm.2005.05.021
Muratovska, 2001, Targeting peptide nucleic acid (PNA) oligomers to mitochondria within cells by conjugation to lipophilic cations: implications for mitochondrial DNA replication, expression and disease, Nucl. Acid. Res, 29, 1852, 10.1093/nar/29.9.1852
Nakamura, 2006, Significant and prolonged antisense effect of a multifunctional envelope-type nano device encapsulating antisense oligodeoxynucleotide, J. Pharm. Pharmacol., 58, 431, 10.1211/jpp.58.4.0002
Newman, 1993, Leber’s hereditary optic neuropathy. New genetic considerations, Arch. Neurol., 50, 540, 10.1001/archneur.1993.00540050082021
Nishikawa, 1989, Long-term coenzyme Q10 therapy for a mitochondrial encephalomyopathy with cytochrome c oxidase deficiency: a 31P NMR study, Neurology, 39, 399, 10.1212/WNL.39.3.399
Oku, 1994, Therapeutic effect of adriamycin encapsulated in long-circulating liposomes on Meth-A-sarcoma-bearing mice, Int. J. Cancer, 58, 415, 10.1002/ijc.2910580318
Otsuka, 1990, Marked decrease of mitochondrial DNA with multiple deletions in a patient with familial mitochondrial myopathy, Biochem. Biophys. Res. Commun., 167, 680, 10.1016/0006-291X(90)92079-F
Owen, 2000, Recombinant adeno-associated virus vector-based gene transfer for defects in oxidative metabolism, Hum. Gene Ther., 11, 2067, 10.1089/104303400750001381
Pfeiffer, 1995, The peptide mastoparan is a potent facilitator of the mitochondrial permeability transition, J. Biol. Chem., 270, 4923, 10.1074/jbc.270.9.4923
Saraste, 1999, Oxidative phosphorylation at the fin de siecle, Science, 283, 1488, 10.1126/science.283.5407.1488
Schatz, 1996, The protein import system of mitochondria, J. Biol. Chem., 271, 31763, 10.1074/jbc.271.50.31763
Scheffler, 2000, A century of mitochondrial research: achievements and perspectives, Mitochondrion, 1, 3, 10.1016/S1567-7249(00)00002-7
Seibel, 1995, Transfection of mitochondria: strategy towards a gene therapy of mitochondrial DNA diseases, Nucl. Acid. Res., 23, 10, 10.1093/nar/23.1.10
Shanske, 1990, Widespread tissue distribution of mitochondrial DNA deletions in Kearns–Sayre syndrome, Neurology, 40, 24, 10.1212/WNL.40.1.24
Shoffner, 1990, Myoclonic epilepsy and ragged-red fiber disease (MERRF) is associated with a mitochondrial DNA tRNA(Lys) mutation, Cell, 61, 931, 10.1016/0092-8674(90)90059-N
Shokolenko, 2003, The expression of exonuclease III from E. coli in mitochondria of breast cancer cells diminishes mitochondrial DNA repair capacity and cell survival after oxidative stress, DNA Repair (Amst), 2, 471, 10.1016/S1568-7864(03)00019-3
Shokolenko, 2005, TAT-mediated protein transduction and targeted delivery of fusion proteins into mitochondria of breast cancer cells, DNA Repair (Amst), 4, 511, 10.1016/j.dnarep.2004.11.009
Smith, 1999, Selective targeting of an antioxidant to mitochondria, Eur. J. Biochem., 263, 709, 10.1046/j.1432-1327.1999.00543.x
Srivastava, 2001, Manipulating mitochondrial DNA heteroplasmy by a mitochondrially targeted restriction endonuclease, Hum. Mol. Genet., 10, 3093, 10.1093/hmg/10.26.3093
Suzuki, 1995, A case of diabetic amyotrophy associated with 3243 mitochondrial tRNA(leu; UUR) mutation and successful therapy with coenzyme Q10, Endocr. J., 42, 141, 10.1507/endocrj.42.141
Taniike, 1992, Mitochondrial tRNA(Ile) mutation in fatal cardiomyopathy, Biochem. Biophys. Res. Commun., 186, 47, 10.1016/S0006-291X(05)80773-9
Tranebjaerg, 1995, A new X linked recessive deafness syndrome with blindness, dystonia, fractures, and mental deficiency is linked to Xq22, J. Med. Genet., 32, 257, 10.1136/jmg.32.4.257
Vestweber, 1989, DNA–protein conjugates can enter mitochondria via the protein import pathway, Nature, 338, 170, 10.1038/338170a0
Wadia, 2003, Modulation of cellular function by TAT mediated transduction of full length proteins, Curr. Protein Pept. Sci., 4, 97, 10.2174/1389203033487289
Weissig, 2001, Cationic bolasomes with delocalized charge centers as mitochondria-specific DNA delivery systems, Adv. Drug Deliv. Rev., 49, 127, 10.1016/S0169-409X(01)00131-4
Yamada, 2005, Development of efficient packaging method of oligodeoxynucleotides by a condensed nano particle in lipid envelope structure, Biol. Pharm. Bull., 28, 1939, 10.1248/bpb.28.1939