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Molecular Therapy

SCOPUS (2000-2023)SCIE-ISI

  1525-0016

 

 

Cơ quản chủ quản:  Cell Press

Lĩnh vực:
Molecular BiologyPharmacologyMedicine (miscellaneous)GeneticsMolecular MedicineDrug Discovery

Các bài báo tiêu biểu

Incorporation of Pseudouridine Into mRNA Yields Superior Nonimmunogenic Vector With Increased Translational Capacity and Biological Stability
Tập 16 Số 11 - Trang 1833-1840 - 2008
Katalin Karikó, Hiromi Muramatsu, Frank A. Welsh, János Ludwig, Hiroki Kato, Shizuo Akira, Drew Weissman
A Novel Nanoparticle Drug Delivery System: The Anti-inflammatory Activity of Curcumin Is Enhanced When Encapsulated in Exosomes
Tập 18 Số 9 - Trang 1606-1614 - 2010
Dongmei Sun, Xiaoying Zhuang, Xiaoyu Xiang, Yuelong Liu, Shuangyin Zhang, Cunren Liu, Stephen Barnes, William E. Grizzle, Donald R. Miller, Huang-Ge Zhang
Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection
Tập 16 Số 6 - Trang 1073-1080 - 2008
Carmela Zincarelli, Stephen Soltys, Giuseppe Rengo, Joseph E. Rabinowitz
T Cells Targeting Carcinoembryonic Antigen Can Mediate Regression of Metastatic Colorectal Cancer but Induce Severe Transient Colitis
Tập 19 Số 3 - Trang 620-626 - 2011
Maria R. Parkhurst, James C. Yang, Russell C. Langan, Mark E. Dudley, Debbie Nathan, Steven A. Feldman, Jeremy L. Davis, Richard A. Morgan, Maria J. Merino, Richard M. Sherry, Marybeth S. Hughes, Udai S. Kammula, Giao Q. Phan, Ramona M. Lim, Stephen A. Wank, Nicholas P. Restifo, Paul F. Robbins, Carolyn M. Laurençot, Steven A. Rosenberg
Cellular Uptake of Arginine-Rich Peptides: Roles for Macropinocytosis and Actin Rearrangement
Tập 10 Số 6 - Trang 1011-1022 - 2004
Ikuhiko Nakase, Miki Niwa, Toshihide Takeuchi, Kazuhiro Sonomura, Noriko Kawabata, Yukihiro Koike, Masanori Takehashi, Seigo Tanaka, Kunihiro Ueda, Jeremy C. Simpson, Arwyn T. Jones, Yukio Sugiura, Shiroh Futaki
Repair of Tissues by Adult Stem/Progenitor Cells (MSCs): Controversies, Myths, and Changing Paradigms
Tập 17 Số 6 - Trang 939-946 - 2009
Darwin J. Prockop
FDA-Approved Oligonucleotide Therapies in 2017
Tập 25 Số 5 - Trang 1069-1075 - 2017
C. A. Stein, Daniela Castanotto
RNA Interference in Vitro and in Vivo Using a Novel Chitosan/siRNA Nanoparticle System
Tập 14 Số 4 - Trang 476-484 - 2006
Kenneth A. Howard, Ulrik L. Rahbek, Xiudong Liu, Christian Kroun Damgaard, Sys Zoffmann Glud, Morten Østergaard Andersen, Mads Bruun Hovgaard, Alexander Schmitz, Jens R. Nyengaard, Flemming Besenbacher, Jørgen Kjems
Current Clinical Applications of In Vivo Gene Therapy with AAVs
Tập 29 Số 2 - Trang 464-488 - 2021
Jerry R. Mendell, Samiah Al-Zaidy, Louise R. Rodino‐Klapac, Kimberly Goodspeed, Steven J. Gray, Christine N. Kay, Sanford L. Boye, Sanford L. Boye, Lindsey A. Greene, Stephanie Salabarria, Manuela Corti, Barry J. Byrne, Jacques P. Tremblay
Dominant-Negative TGF-β Receptor Enhances PSMA-Targeted Human CAR T Cell Proliferation And Augments Prostate Cancer Eradication
Tập 26 Số 7 - Trang 1855-1866 - 2018
Christopher C. Kloss, Ji‐Hyun Lee, Aaron Zhang, Fang Chen, J. Joseph Melenhorst, Simon F. Lacey, Marcela V. Maus, Joseph A. Fraietta, Yangbing Zhao, Carl H. June