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Molecular Therapy

  1525-0016

 

 

Cơ quản chủ quản:  Cell Press

Lĩnh vực:
Molecular BiologyPharmacologyMedicine (miscellaneous)GeneticsMolecular MedicineDrug Discovery

Các bài báo tiêu biểu

Successful Treatment of UGT1A1 Deficiency in a Rat Model of Crigler–Najjar Disease by Intravenous Administration of a Liver-Specific Lentiviral Vector
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Pascal van der Wegen, Rogier Louwen, Ali M. Imam, Ruvalic M. Buijs-Offerman, Maarten Sinaasappel, Frank Grosveld, Bob J. Scholte
Use of miRNA Response Sequences to Block Off-target Replication and Increase the Safety of an Unattenuated, Glioblastoma-targeted Oncolytic HSV
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Lucia Mazzacurati, Marco Marzulli, Bonnie Reinhart, Yoshitaka Miyagawa, Hiroaki Uchida, William F Goins, Aofei Li, Balveen Kaur, Michael Caligiuri, Timothy Cripe, Nino Chiocca, Nduka Amankulor, Justus B Cohen, Joseph C Glorioso, Paola Grandi
Cancer Stem Cell–Directed Therapies: Recent Data From the Laboratory and Clinic
Tập 17 - Trang 219-230 - 2009
Christopher Y Park, Diane Tseng, Irving L Weissman
Precise excision of HTLV-1 provirus with a designer-recombinase
Tập 31 - Trang 2266-2285 - 2023
Teresa Rojo-Romanos, Janet Karpinski, Sebastian Millen, Niklas Beschorner, Florian Simon, Maciej Paszkowski-Rogacz, Felix Lansing, Paul Martin Schneider, Jan Sonntag, Joachim Hauber, Andrea K. Thoma-Kress, Frank Buchholz
Muscle-Directed Gene Transfer and Transient Immune Suppression Result in Sustained Partial Correction of Canine Hemophilia B Caused by a Null Mutation
Tập 4 - Trang 192-200 - 2001
Roland W. Herzog, Jane D. Mount, Valder R. Arruda, Katherine A. High, Clinton D. Lothrop
A two-stage poly(ethylenimine)-mediated cytotoxicity: implications for gene transfer/therapy
Tập 11 - Trang 990-995 - 2005
S. Moein Moghimi, Peter Symonds, J. Clifford Murray, A. Christy Hunter, Grazyna Debska, Adam Szewczyk
Guanidinylated Neomycin Mediates Heparan Sulfate–dependent Transport of Active Enzymes to Lysosomes
Tập 18 - Trang 1268-1274 - 2010
Stéphane Sarrazin, Beth Wilson, William S Sly, Yitzhak Tor, Jeffrey D Esko
A chimeric human/dog-DNA vaccine against CSPG4 induces immunity with therapeutic potential in comparative preclinical models of osteosarcoma
Tập 31 - Trang 2342-2359 - 2023
Lidia Tarone, Davide Giacobino, Mariateresa Camerino, Lorella Maniscalco, Selina Iussich, Lorenza Parisi, Giuseppe Giovannini, Alfredo Dentini, Elisabetta Bolli, Elena Quaglino, Irene Fiore Merighi, Emanuela Morello, Paolo Buracco, Federica Riccardo, Federica Cavallo