Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection
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Berns, 1995, The cryptic life style of adeno-associated virus, Bioassays, 17, 237, 10.1002/bies.950170310
Bartlett, 2000, Infectious entry pathway of adeno-associated virus and adeno-associated virus vectors, J Virol, 74, 2777, 10.1128/JVI.74.6.2777-2785.2000
Duan, 1999, Dynamin is required for recombinant adeno-associated virus type 2 infection, J Virol, 73, 10371, 10.1128/JVI.73.12.10371-10376.1999
Douar, 2001, Intracellular trafficking of adeno-associated virus vectors: routing to the late endosomal compartment and proteasome degradation, J Virol, 75, 1824, 10.1128/JVI.75.4.1824-1833.2001
Thomas, 2004, Rapid uncoating of vector genomes is the key to efficient liver transduction with pseudotyped adeno-associated virus vectors, J Virol, 78, 3110, 10.1128/JVI.78.6.3110-3122.2004
Chiorini, 1997, Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles, J Virol, 71, 6823, 10.1128/JVI.71.9.6823-6833.1997
Rutledge, 1998, Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2, J Virol, 72, 309, 10.1128/JVI.72.1.309-319.1998
Chiorini, 1999, Cloning and characterization of adeno-associated virus type 5, J Virol, 73, 1309, 10.1128/JVI.73.2.1309-1319.1999
Gao, 2002, Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy, Proc Natl Acad Sci USA, 99, 11854, 10.1073/pnas.182412299
Gao, 2004, Clades of adeno-associated viruses are widely disseminated in human tissues, J Virol, 78, 6381, 10.1128/JVI.78.12.6381-6388.2004
Gao, 2003, Adeno-associated viruses undergo substantial evolution in primates during natural infections, Proc Natl Acad Sci USA, 100, 6081, 10.1073/pnas.0937739100
Rabinowitz, 2002, Cross-packaging of single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity, J Virol, 76, 791, 10.1128/JVI.76.2.791-801.2002
Burger, 2004, Recombinant AAV viral vectors pseudotyped with viral capsids from serotypes 1, 2, and 5 display differential efficiency and cell tropism after delivery to different regions of the central nervous system, Mol Ther, 10, 302, 10.1016/j.ymthe.2004.05.024
Cearley, 2006, Transduction characteristics of adeno-associated virus vectors expressing cap serotypes 7, 8, 9, and Rh10 in the mouse brain, Mol Ther, 13, 528, 10.1016/j.ymthe.2005.11.015
Taymans, 2007, Comparative analysis of adeno-associated viral vector serotypes 1, 2, 5, 7, and 8 in mouse brain, Hum Gene Ther, 18, 195, 10.1089/hum.2006.178
Sondhi, 2007, Enhanced survival of the LINCL mouse following CLN2 gene transfer using the rh.10 rhesus macaque-derived adeno-associated virus vector, Mol Ther, 15, 481, 10.1038/sj.mt.6300049
Klein, 2008, AAV8, 9, Rh10, Rh43 vector gene transfer in the rat brain: effects of serotype, promoter and purification method, Mol Ther, 16, 89, 10.1038/sj.mt.6300331
White, 2004, Targeted gene delivery to vascular tissue in vivo by tropism-modified adeno-associated virus vectors, Circulation, 109, 513, 10.1161/01.CIR.0000109697.68832.5D
Work, 2006, Vascular bed-targeted in vivo gene delivery using tropism-modified adeno-associated viruses, Mol Ther, 13, 683, 10.1016/j.ymthe.2005.11.013
Halbert, 2000, Repeat transduction in the mouse lung by using adeno-associated virus vectors with different serotypes, J Virol, 74, 1524, 10.1128/JVI.74.3.1524-1532.2000
Halbert, 2001, Adeno-associated virus type 6 (AAV6) vectors mediate efficient transduction of airway epithelial cells in mouse lungs compared to that of AAV2 vectors, J Virol, 75, 6615, 10.1128/JVI.75.14.6615-6624.2001
Grimm, 2006, Liver transduction with recombinant adeno-associated virus is primarily restricted by capsid serotype not vector genotype, J Virol, 80, 426, 10.1128/JVI.80.1.426-439.2006
Gao, 2006, High-level transgene expression in nonhuman primate liver with novel adeno-associated virus serotypes containing self-complementary genomes, J Virol, 80, 6192, 10.1128/JVI.00526-06
Inagaki, 2006, Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8, Mol Ther, 14, 45, 10.1016/j.ymthe.2006.03.014
Nakai, 2005, Large-scale molecular characterization of adeno-associated virus vector integration in mouse liver, J Virol, 79, 3606, 10.1128/JVI.79.6.3606-3614.2005
Chao, 2000, Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors, Mol Ther, 2, 619, 10.1006/mthe.2000.0219
Blankinship, 2004, Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6, Mol Ther, 10, 671, 10.1016/j.ymthe.2004.07.016
Wang, 2005, Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart, Nat Biotechnol, 23, 321, 10.1038/nbt1073
Li, 2003, Efficient and long-term intracardiac gene transfer in delta-sarcoglycan-deficienty hamster by adeno-associated virus-2 vectors, Gene Ther, 10, 1807, 10.1038/sj.gt.3302078
Gregorevic, 2004, Systemic delivery of genes to striated muscles using adeno-associated viral vectors, Nat Med, 10, 828, 10.1038/nm1085
Müller, 2006, Improved cardiac gene transfer by transcriptional and transductional targeting of adeno-associated viral vectors, Cardiovasc Res, 70, 70, 10.1016/j.cardiores.2005.12.017
Pacak, 2006, Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo, Circ Res, 99, e3, 10.1161/01.RES.0000237661.18885.f6
Palomeque, 2007, Efficiency of eight different AAV serotypes in transducing rat myocardium in vivo, Gene Ther, 14, 989, 10.1038/sj.gt.3302895
Wu, 2001, Noninvasive optical imaging of firefly luciferase reporter gene expression in skeletal muscles of living mice, Mol Ther, 4, 297, 10.1006/mthe.2001.0460
Lipshutz, 2001, In utero delivery of adeno-associated viral vectors: intraperitoneal gene transfer produces long-term expression, Mol Ther, 3, 284, 10.1006/mthe.2001.0267
Nathwani, 2007, Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates, Blood, 109, 1414, 10.1182/blood-2006-03-010181
Sarkar, 2004, Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype, Blood, 103, 1253, 10.1182/blood-2003-08-2954
Grimm, 2003, Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy, Blood, 102, 2412, 10.1182/blood-2003-02-0495
Haberman, 1999, Production of recombinant adeno-associated viral vectors and use in vitro and in vivo administration, 4.17.1