Clinical and neuroimaging findings in 33 patients with MCAP syndrome: A survey to evaluate relevant endpoints for future clinical trialsClinical Genetics - Tập 99 Số 5 - Trang 650-661 - 2021
Aurore Garde, Laurent Guibaud, Alice Goldenberg, Florence Petit, Rodolphe Dard, J. Roume, J. Mazereeuw‐Hautier, Nicolas Chassaing, Didier Lacombe, Fanny Morice‐Picard, Annick Toutain, Stéphanie Arpin, O. Boccara, Renaud Touraine, Patricia Blanchet, Christine Coubes, Marjolaine Willems, Lucile Pinson, Philippe Khau Van Kien, C. Chiavérini, Fabienne Giuliano, Jean‐Luc Alessandri, Michèle Mathieu‐Dramard, Gilles Morin, A.‐C. Bursztejn, Cyril Mignot, Diane Doummar, Frederico Di Rocco, Jenny Cornaton, Claire Nicolas, Élodie Gautier, Maxime Luu, Marc Bardou, Arthur Sorlin, Christophe Philippe, Patrick Edery, Massimiliano Rossi, Virginie Carmignac, Christel Thauvin‐Robinet, P. Vabres, Laurence Faivre