Ten-year-long enzyme replacement therapy shows a poor effect in alleviating giant leg ulcers in a male with Fabry disease

Molecular Genetics and Metabolism Reports - Tập 14 - Trang 68-72 - 2018
Jun Okada1, Mohammad Arif Hossain2,3, Chen Wu2, Takashi Miyajima2, Hiroko Yanagisawa2, Keiko Akiyama2, Yoshikatsu Eto2,3
1Asakadai Central General Hospital, Asaka City, Japan
2Advanced Clinical Research Center, Institute of Neurological Disorders, Shin-Yurigaoka General Hospital, Kawasaki, Kanagawa, Japan
3Department of Gene Therapy, Institute for DNA Medicine, The Jikei University School of Medicine, Tokyo, Japan

Tài liệu tham khảo

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