Recombinant Adeno-Associated Virus Vector-Based Gene Transfer for Defects in Oxidative Metabolism

Human Gene Therapy - Tập 11 Số 15 - Trang 2067-2078 - 2000
Renius Owen1, Alfred S. Lewin2, Alyson Peel3, Jianming Wang4, John Guy5, William W. Hauswirth6, Peter W. Stacpoole7, Terence R. Flotte8
1Department of Pediatrics; Department of Molecular Genetics and Microbiology; Department of Biochemistry and Molecular Biology; Center for Mammalian Genetics, University of Florida, Gainesville, FL 32610
2Department of Molecular Genetics and Microbiology; Center for Mammalian Genetics; Gene Therapy Center, University of Florida, Gainesville, FL 32610
3Gene Therapy Center; Department of Neuroscience, University of Florida, Gainesville, FL 32610
4Department of Pediatrics; Department of Molecular Genetics and Microbiology; Gene Therapy Center, University of Florida, Gainesville, FL 32610
5Department of Ophthalmology, Department of Medicine, University of Florida, Gainesville, FL 32610
6Department of Molecular Genetics and Microbiology; Gene Therapy Center; Department of Ophthalmology, University of Florida, Gainesville, FL 32610
7Department of Biochemistry and Molecular Biology; Department of Medicine, University of Florida, Gainesville, FL 32610
8Department of Pediatrics; Department of Molecular Genetics and Microbiology; Center for Mammalian Genetics; Gene Therapy Center, University of Florida, Gainesville, FL 32610

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