Muscle Function Recovery in Golden Retriever Muscular Dystrophy After AAV1-U7 Exon Skipping

Molecular Therapy - Tập 20 - Trang 2120-2133 - 2012
Adeline Vulin1,2, Inès Barthélémy3, Aurélie Goyenvalle1, Jean-Laurent Thibaud3, Cyriaque Beley1, Graziella Griffith1, Rachid Benchaouir1, Maëva le Hir1, Yves Unterfinger3, Stéphanie Lorain1, Patrick Dreyfus1, Thomas Voit1, Pierre Carlier4, Stéphane Blot1,3, Luis Garcia1
1UPMC Um76, Inserm U974, CNRS UMR7215, Institut de Myologie, 105 Bd de l'Hôpital, Paris, France
2Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, USA
3Université Paris Est, Ecole Nationale Vétérinaire d'Alfort, UPR de Neurobiologie, Maisons Alfort, France
4Laboratoire RMN AIM-CEA, Institut de Myologie, Hôpital Pitié-Salpêtrière, Paris, France

Tài liệu tham khảo

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