Muscle-Directed Gene Transfer and Transient Immune Suppression Result in Sustained Partial Correction of Canine Hemophilia B Caused by a Null Mutation

Molecular Therapy - Tập 4 - Trang 192-200 - 2001
Roland W. Herzog1, Jane D. Mount2, Valder R. Arruda1, Katherine A. High1, Clinton D. Lothrop2
1Departments of Pediatrics and Pathology, University of Pennsylvania Medical Center and The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, 19104, USA
2Scott-Ritchey Research Center and Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, Alabama, 36849, USA

Tài liệu tham khảo

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