Human Homolog of patched , a Candidate Gene for the Basal Cell Nevus Syndrome

American Association for the Advancement of Science (AAAS) - Tập 272 Số 5268 - Trang 1668-1671 - 1996
Ronald L. Johnson1, Alana Rothman2, Jingwu Xie2, Lisa V. Goodrich1, John W. Bare2, Jeannette M. Bonifas2, Anthony G. Quinn2, R Myers3, David R. Cox3, Ervin H. Epstein2, Matthew P. Scott1
1R. L. Johnson, L. V. Goodrich, M. P. Scott, Departments of Developmental Biology and Genetics, Howard Hughes Medical Institute, Stanford University School of Medicine, Stanford, CA 94305-5427, USA.
2A. L. Rothman, J. Xie, J. W. Bare, J. M. Bonifas, A. G. Quinn, E. H. Epstein Jr., Department of Dermatology, San Francisco General Hospital, University of California, San Francisco, CA 94110, USA.
3R. M. Myers and D. R. Cox, Department of Genetics, Stanford University School of Medicine, Stanford, CA 94305, USA.

Tóm tắt

The basal cell nevus syndrome (BCNS) is characterized by developmental abnormalities and by the postnatal occurrence of cancers, especially basal cell carcinomas (BCCs), the most common human cancer. Heritable mutations in BCNS patients and a somatic mutation in a sporadic BCC were identified in a human homolog of the Drosophila patched (ptc) gene. The ptc gene encodes a transmembrane protein that in Drosophila acts in opposition to the Hedgehog signaling protein, controlling cell fates, patterning, and growth in numerous tissues. The human PTC gene appears to be crucial for proper embryonic development and for tumor suppression.

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