Enhancing Muscle Membrane Repair by Gene Delivery of MG53 Ameliorates Muscular Dystrophy and Heart Failure in δ-Sarcoglycan-deficient Hamsters

Molecular Therapy - Tập 20 - Trang 727-735 - 2012
Bo He1, Ru-hang Tang1, Noah Weisleder2, Bin Xiao1, Zhenhua Yuan1, Chuanxi Cai2, Hua Zhu2, Peihui Lin2, Chunping Qiao1, Jianbin Li1, Christina Mayer1, Juan Li1, Jianjie Ma2, Xiao Xiao1
1Division of Molecular Pharmaceutics, University of North Carolina Eshelman School of Pharmacy, Chapel Hill, North Carolina, USA
2Department of Physiology and Biophysics, Robert Wood Johnson Medical School, Piscataway, New Jersey, USA

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