Comparison of Adeno-Associated Virus Pseudotype 1, 2, and 8 Vectors Administered by Intramuscular Injection in the Treatment of Murine Phenylketonuria

Human Gene Therapy - Tập 21 Số 4 - Trang 463-477 - 2010
Alexandre Rebuffat1, Cary O. Harding2, Zhaobing Ding1,3, Beat Thöny1
1Division of Clinical Chemistry and Biochemistry, Department of Pediatrics, University of Zürich, CH-8032 Zürich, Switzerland.
2Department of Molecular and Medical Genetics, Oregon Health and Science University, Portland, OR 97201, USA
3Present address: Institute of Bioengineering and Nanotechnology, The Nanos, 138669, Singapore.

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