Arylsulfatase A Overexpressing Human iPSC-derived Neural Cells Reduce CNS Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy

Molecular Therapy - Tập 23 - Trang 1519-1531 - 2015
Jonas Doerr1, Annika Böckenhoff2, Benjamin Ewald1, Julia Ladewig1, Matthias Eckhardt2, Volkmar Gieselmann2, Ulrich Matzner2, Oliver Brüstle1, Philipp Koch1
1Institute of Reconstructive Neurobiology, Life & Brain Center, University of Bonn, Bonn, Germany
2Institute of Biochemistry and Molecular Biology, University of Bonn, Bonn, Germany

Tài liệu tham khảo

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