Abnormal fatty acid composition of biotin-responsive multiple carboxylase deficiency fibroblasts

Journal of Inherited Metabolic Disease - Tập 12 - Trang 47-57 - 1989
S. Packman1, S. C. Whitney1, M. Fitch2, S. E. Fleming2
1Division of Genetics, Department of Pediatrics, University of California, San Francisco
2Department of Nutritional Sciences, University of California, Berkeley, USA.

Tóm tắt

Clinical and biochemical correlations in the biotin-responsive multiple carboxylase deficiencies have suggested that disordered lipogenesis plays a role in the pathogenesis of the disease. In particular, the activity of biotin-dependent acetyl CoA carboxylase and thede novo synthesis of fatty acids are reduced in mutant fibroblasts. In the present work, we examine the biochemical consequences of these deficiencies, and document and characterize an abnormal fatty acid composition in holocarboxylase synthetase deficiency fibroblasts. Following growth in biotin-restricted medium, the total fatty acid content of mutant cells is reduced. There were significant reductions in the percentage as 16:0, 18:0 and 20:3N9 fatty acids, with the proportion of longer-chain fatty acids either increased or maintained at control levels. The cellular content of 16:0, 16:1, 18:0, 18:1 and 20:3N9 fatty acids was reduced, while that of the longer-chain fatty acids was preserved at control levels in mutant cells deprived of biotin. We speculate that the components of the altered fatty acid pools may be disproportionately incorporated into complex lipids in mutant cells, with pathologic effects on the multiple carboxylase deficiency phenotype.

Tài liệu tham khảo

Bartlett, K. and Gompertz, D. Biotin activation of carboxylase activity in cultured fibroblasts.Clin. Chim. Acta 84 (1978) 399–401 Blom, W., de Muinck Keizer, S. and Scholte, H. Acetyl CoA carboxylase deficiency: an inborn error ofde novo fatty acid synthesis.N. Engl. J. Med. 305 (1981) 465–466 Burri, B., Sweetman, L. and Nyhan, W. Mutant holocarboxylase synthetase: evidence for the enzyme defect in early infantile biotin-responsive multiple carboxylase deficiency.J. Clin. Invest. 68 (1981) 1491–1495 Cowan, M., Wara, D., Packman, S., Ammann, A., Yoshino, M., Sweetman, L. and Nyhan, W. Multiple biotin dependent carboxylase deficiencies associated with defects in T and B cell immunity.Lancet 2 (1979) 115–118 Crocker, P., Fitch, M. and Ostwald, R. Effects of the unsaturation of dietary fat and of arachidonate supplementation on cholesterol pool expansion in the guinea pig.J. Nutr. 109 (1979) 927–938 Dixon, W. and Massey, F. Jr.Introduction to Statistical Analysis. McGraw-Hill, New York, 1969 Donaldson, W. Biotin effects on fatty acids synthesis in chicks.Ann. NY Acad. Sci. 447 (1985) 104–111 Feldman, G. and Wolf, B. Deficient acetyl CoA carboxylase activity in multiple carboxylase deficiency.Clin. Chim. Acta 111 (1981) 147–151 Fretag, S. and Utter, M. Introduction of pyruvate carboxylase in 3T3-L1 cells.Proc. Natl. Acad. Sci. USA 77 (1980) 1321–1325 Ginsburg, R., Robertson, A. and Michel, B. Acrodermatitis enteropathica: abnormalities of fat metabolism.Arch. Dermatol. 112 (1976) 653–660 Gonzalez-Rios, M. C., Whitney, S., Williams, M., Elias, P. and Packman, S. Lipid metabolism in biotin-responsive multiple carboxylase deficiency.J. Inher. Metab. Dis. 8 (1985) 184–186 Kim, K. H. Control of acetyl-CoA carboxylase by covalent modification.Mol. Cell Biochem. 28 (1979) 28–43 Markwell, M., Haas, S., Bieber, L. and Tolbert, N. A modification of the Lowry procedure to simplify protein determination in membrane acid lipoprotein samples.Anal. Biochem. 87 (1978) 206–210 Mock, D., deLorimer, A., Liebman, W., Sweetman, L. and Baker, H. Biotin deficiency: an unusual complication of parenteral alimentation.N. Engl. J. Med. 304 (1981) 820–823 Munnich, A., Saudubray, J., Coude, F., Charpentier, C., Saurat, J. and Frezal, J. Fattyacid responsive alopecia in multiple carboxylase deficiency.Lancet 1 (1980) 1080–1081 Ostwald, R., Yamanaka, W. and Light, M. The phospholipids of liver, plasma and red cells in guinea pigs.Proc. Soc. Exp. Biol. Med. 1345 (1970) 814–820 Packman, S., Caswell, N. and Baker, H. Biochemical evidence for diverse etiologies in biotin-responsive multiple carboxylase deficiency.Biochem. Genet. 20 (1982a) 17–28 Packman, S., Caswell, N., Gonzalez-Rios, M. C., Kadlecek, T., Cann, H., Rassin, D. and McKay, C. Acetyl CoA carboxylase in cultured fibroblasts: differential biotin dependence in the two types of biotin-responsive multiple carboxylase deficiency.Am. J. Hum. Genet. 36 (1984) 80–92 Packman, S., Cowan, M., Golbus, M., Caswell, N., Sweetman, S., Burri, B., Nyhan, W. and Baker, H. Prenatal treatment of biotin-responsive multiple carboxylase deficiency.Lancet 1 (1982b) 1435–1439 Packman, S., Sweetman, L., Baker, H. and Wall, S. The neonatal form of biotin-responsive multiple carboxylase deficiency.J. Pediatr. 99 (1981) 418–420 Proud, V., Patterson, J., Rizzo, W. and Wolf, B. Skin abnormalities in biotinidase deficiency may be associated with alterations in fatty acid composition.Am. J. Hum. Genet. 39 (1986) A18 Sander, J., Malamud, N., Cowan, M., Packman, S., Ammann, A. and Wara, D. Intermittent ataxia, organic aciduria and immunodeficiency: a vitamin responsive disorder.Ann. Neurol. 8 (1980) 544–547 Saunders, M., Sherwood, W., Duthie, M., Surh, L. and Gravel, R. Evidence for a defect of holocarboxylase synthetase activity in cultured lymphoblasts from a patient with biotinresponsive multiple carboxylase deficiency.Am. J. Hum. Genet. 34 (1982) 590–601 Shafrir, E. and Bierman, E. Acetyl-CoA carboxylase activity in cultured human fibroblasts: induction by insulin in relation to cell growth and triacylglycerol metabolism.Biochim. Biophys. Acta 663 (1981) 432–445 Sweetman, L., Bates, S., Hull, D. and Nyhan, W. Propionyl CoA carboxylase deficiency in a patient with biotin-responsive 3-methylcrotonyl glycinuria.Pediatr. Res. 11 (1977) 1144–1147 Sweetman, L. and Nyhan, W. Inheritable biotin-treatable disorders and associated phenomena.Annu. Rev. Nutr. 6 (1986) 317–343 Thompson, G.The Regulation of Membrane Lipid Metabolism. CRC Press, Boca Raton, 1980 Williams, M., Packman, S. and Cowan, M. Alopecia and periorificial dermatitis in biotinresponsive multiple carboxylase deficiency.J. Am. Acad. Dermatol. 9 (1983) 97–103 Wolf, B., Grier, R., Allen, R., Goodman, S. and Kien, C. Biotinidase deficiency: the enzymatic defect in late-onset multiple carboxylase deficiency.Clin. Chim. Acta 131 (1983) 273–281