A window of opportunity trial evaluating intratumoral injection of Copaxone® in patients with percutaneously accessible tumors

Translational Medicine Communications - Tập 8 - Trang 1-9 - 2023
Joaquina C. Baranda1, Ghulam Rehman Mohyuddin2, Andrés M. Bur3, Yelizaveta Shnayder3, Kyle R. Sweeney4, Kiran Kakarala3, Megan Prouty5, Harsh Pathak6,7, Rajni Puri6, Amrita Mitra6, Rashna Madan6, M. Laird Forrest8, Aric Huang8, Scott Weir9, Andrew K. Godwin6,7, Nabil A. Alhakamy10,11,12,13, J. Daniel Griffin13, Cory J. Berkland8,13,14
1Clinical Research Center, University of Kansas Comprehensive Cancer Center, Fairway, USA
2Division of Hematology and Hematological Malignancies, Huntsman Cancer Institute, University of Utah, Salt Lake City, USA
3Department of Otolaryngology-Head and Neck Surgery, University of Kansas Medical Center, Kansas City, USA
4Department of Orthopedic Surgery and Sports Medicine, Sarcoma Center, University of Kansas Comprehensive Cancer Center, Kansas City, USA
5Department of Dermatology, University of Utah, Salt Lake City, USA
6Department of Pathology and Laboratory Medicine, Medical Center, University of Kansas, Kansas City, USA
7Kansas Institute for Precision Medicine, Medical Center, University of Kansas, Kansas City, USA
8Department of Pharmaceutical Chemistry, University of Kansas, Lawrence, USA
9Institute for Advancing Medical Innovation, Medical Center, University of Kansas, Kansas City, USA
10Department of Pharmaceutics, Faculty of Pharmacy, King Abdulaziz University, Jeddah, Saudi Arabia
11Center of Excellence for Drug Research and Pharmaceutical Industries, King Abdulaziz University, Jeddah, Saudi Arabia
12Mohamed Saeed Tamer Chair for Pharmaceutical Industries, Faculty of Pharmacy, King Abdulaziz University, Jeddah, Saudi Arabia
13Kinimmune, Inc, St. Louis, USA
14Department of Chemical and Petroleum Engineering, University of Kansas, Lawrence, USA

Tóm tắt

This window of opportunity trial evaluated the safety of intratumoral Copaxone® and profiled immune markers in biopsies before and after treatment. Patients with percutaneously accessible malignancies scheduled for surgical resection with curative intent were eligible to participate. Adverse events from one, two, or three injections of Copaxone® were monitored leading up to surgical resection. Using RNA sequencing and spatial protein profiling of immune-related targets, changes in mRNA and protein expression patterns, respectively were assessed in tumor biopsy samples pre- and post-treatment. Adverse events at the injection site were mild and consistent with historic subcutaneous administration of Copaxone®. Increased intratumoral immune activity was evident in most patients, including the upregulation of genes associated with immune stimulation and targets of checkpoint inhibitor therapy. Intratumoral injection of Copaxone® was well tolerated, and immune profile changes in the tumor microenvironment warrant its further evaluation as human intratumoral immunotherapy. clinicaltrials.gov, NCT03982212 First posted June 11th, 2019

Tài liệu tham khảo

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