A comparison of robust Mendelian randomization methods using summary data

Genetic Epidemiology - Tập 44 Số 4 - Trang 313-329 - 2020
Eric A. W. Slob1,2, Stephen Burgess3,4
1Erasmus School of Economics, Erasmus University Rotterdam, Rotterdam, The Netherlands
2Erasmus University Rotterdam Institute for Behavior and Biology, Rotterdam, The Netherlands
3Department of Public Health and Primary Care, University of Cambridge, Cambridge, UK
4MRC Biostatistics Unit, University of Cambridge, Cambridge, UK

Tóm tắt

Abstract

The number of Mendelian randomization (MR) analyses including large numbers of genetic variants is rapidly increasing. This is due to the proliferation of genome‐wide association studies, and the desire to obtain more precise estimates of causal effects. Since it is unlikely that all genetic variants will be valid instrumental variables, several robust methods have been proposed. We compare nine robust methods for MR based on summary data that can be implemented using standard statistical software. Methods were compared in three ways: by reviewing their theoretical properties, in an extensive simulation study, and in an empirical example. In the simulation study, the best method, judged by mean squared error was the contamination mixture method. This method had well‐controlled Type 1 error rates with up to 50% invalid instruments across a range of scenarios. Other methods performed well according to different metrics. Outlier‐robust methods had the narrowest confidence intervals in the empirical example. With isolated exceptions, all methods performed badly when over 50% of the variants were invalid instruments. Our recommendation for investigators is to perform a variety of robust methods that operate in different ways and rely on different assumptions for valid inferences to assess the reliability of MR analyses.

Từ khóa


Tài liệu tham khảo

10.1093/biostatistics/kxy027

10.1002/gepi.21965

10.1002/sim.7221

Burgess S. Bowden J. Dudbridge F. &Thompson S. G.(2016).Robust instrumental variable methods using multiple candidate instruments with application to Mendelian randomization. arXiv 1606.03279.

10.1002/gepi.21758

10.1002/sim.6835

Burgess S., 2020, A robust and efficient method for Mendelian randomization with hundreds of genetic variants, Nature Communications, 11

10.1007/s10654-017-0255-x

10.1093/ije/dyy080

10.1093/ije/dyg070

10.1177/0962280206077743

10.1073/pnas.1707388115

10.1093/aje/kwr323

10.1111/rssb.12275

10.1093/ije/dyx102

10.3945/ajcn.115.118216

Jiang L., 2017, Constrained instruments and their application to mendelian randomization with pleiotropy, bioRxiv, 22754

10.1080/01621459.2014.994705

10.1038/nature14177

10.1186/s12863-016-0425-y

Mosteller F., 1977, Data analysis and regression: A second course in statistics

10.1038/ng.3396

10.1038/s41588-018-0255-0

10.1093/ije/dyn080

10.1093/aje/kwt084

Qi G., 2019, A comprehensive evaluation of methods for Mendelian randomization using realistic simulations and an analysis of 38 biomarkers for risk of type‐2 diabetes, bioRxiv, 70287

Qi G., 2020, Mendelian randomization analysis using mixture models for robust and efficient estimation of causal effects, Nature Communications, 10

10.1016/j.ajhg.2011.10.004

10.1093/ije/dyh132

10.1038/nrg3461

10.1093/bioinformatics/btw373

Tchetgen Tchetgen E. J. Sun B. &Walter S.(2017).The GENIUS approach to robust Mendelian randomization inference.arXiv 1709.07779 [stat.ME].

10.1016/j.annepidem.2006.12.005

10.1097/EDE.0000000000000081

10.1038/s41588-018-0099-7

10.1016/j.jhealeco.2015.10.007

10.1093/nar/gkt1229

Windmeijer F. Farbmacher H. Davies N. &DaveySmith G.(2016).On the use of the lasso for instrumental variables estimation with some invalid instruments(Technical Report Discussion Paper 16/674). University of Bristol.

Zhao Q. Wang J. Bowden J. &Small D. S.(2018).Statistical inference in two‐sample summary‐data Mendelian randomization using robust adjusted profile score.arXiv 1801.09652 [stat.AP].

10.1093/bioinformatics/btw613