Generation of a Mouse with Low Galactocerebrosidase Activity by Gene Targeting: A New Model of Globoid Cell Leukodystrophy (Krabbe Disease)

Molecular Genetics and Metabolism - Tập 73 - Trang 211-223 - 2001
Paola Luzi1, Mohammad A. Rafi1, Mariam Zaka1, Mark Curtis2, Marie T. Vanier3, David A. Wenger1
1Department of Neurology, Jefferson Medical College, Philadelphia, Pennsylvania
2Department of Pathology, Jefferson Medical College, Philadelphia, Pennsylvania
3INSERM U 189, Lyon-Sud Medical School and Fondation Gillet-Merieux, Lyon-Sud Hospital, Pierre Benite, France

Tài liệu tham khảo

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