Production of Recombinant Adeno-associated Virus Vectors Using Suspension HEK293 Cells and Continuous Harvest of Vector From the Culture Media for GMP FIX and FLT1 Clinical Vector

Molecular Therapy - Tập 24 - Trang 287-297 - 2016
Joshua C Grieger1,2,3, Stephen M Soltys1, Richard Jude Samulski1,4
1Gene Therapy Center, University of North Carolina, Chapel Hill, North Carolina, USA
2Department of Ophthalmology, University of North Carolina, Chapel Hill, North Carolina, USA
3Present address: Bamboo Therapeutics, Inc, Chapel Hill, North Carolina, USA
4Department of Pharmacology, University of North Carolina, Chapel Hill, North Carolina, USA

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