Efficacy and safety of adeno‐associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy

Journal of Thrombosis and Haemostasis - Tập 5 Số 1 - Trang 16-24 - 2007
Thierry VandenDriessche1, Lieven Thorrez1, Abel Acosta‐Sanchez1, Inge Petrus1, Lili Wang2, Ling Ma1, Liesbeth De Waele1, Yasushi Iwasaki1, Veerle Gillijns1, James M. Wilson2, Désiré Collen1, Marinee Chuah1
1Center for Transgene Technology and Gene Therapy, Flanders Interuniversity Institute for Biotechnology, University of Leuven, Leuven, Belgium
2Division of Medical Genetics, Department of Medicine, University of Pennsylvania, Philadelphia, PA, USA

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