ECHS1 mutations in Leigh disease: a new inborn error of metabolism affecting valine metabolism

Brain - Tập 137 Số 11 - Trang 2903-2908 - 2014
Heidi Peters1, Nicole E. Buck1, Ronald J. A. Wanders2, Jos P.N. Ruiter2, Hans R. Waterham2, Janet Koster2, Joy Yaplito‐Lee1, Sacha Ferdinandusse2, James Pitt1,3
11 Murdoch Childrens Research Institute, Victorian Clinical Genetics Services, Royal Children’s Hospital, Parkville, Vic 3052, Australia
22 University of Amsterdam, Laboratory Genetic Metabolic Diseases, Departments of Paediatrics and Laboratory Medicine, Academic Medical Centre, Amsterdam, The Netherlands
33 Department of Paediatrics, University of Melbourne, Parkville, Vic 3052, Australia

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