P.92 UMINESCE: Phase 3 study of satralizumab, a therapeutic recycling antibody targeting the IL-6 receptor, in patients with generalised myasthenia gravisNeuromuscular Disorders - Tập 32 - Trang S80-S81 - 2022
H. Kaminski, C. Zhao, G. Meyer zu Horste, K. O'Connor, G. Klingelschmitt, P. Krumova, S. Bolt, I. Vodopivec, H. Murai
Age and baseline values predict 12 and 24-month functional changes in type 2 SMANeuromuscular Disorders - Tập 30 - Trang 756-764 - 2020
Giorgia Coratti, Maria C Pera, Simona Lucibello, Jacqueline Montes, Amy Pasternak, Anna Mayhew, Allan M Glanzman, Sally Dunaway Young, Marika Pane, Mariacristina Scoto, Sonia Messina, Nathalie Goemans, Andres Nascimiento Osorio, Marina Pedemonte, Valeria Sansone, Enrico Bertini, Darryl C. De Vivo, Richard Finkel, Francesco Muntoni, Eugenio Mercuri
D.O.3 Next generation sequencing applications are ready for genetic diagnosis of muscular dystrophiesNeuromuscular Disorders - Tập 22 - Trang 806 - 2012
M. Savarese, A. Torella, M. Mutarelli, M. Dionisi, T. Giugliano, G. Di Fruscio, M. Iacomino, A. Garofalo, S. Aurino, F. Del Vecchio Blanco, G. Piluso, L. Politano, M. Fanin, C. Angelini, V. Nigro