Enhancement of factor VIIa haemostatic efficacy by formulation with PEGylated liposomesHaemophilia - Tập 14 Số 3 - Trang 476-483 - 2008
Rivka Yatuv, I. DAYAN, Lea Carmel-Goren, Micah Robinson, Irit Aviv, Mirela Goldenberg-Furmanov, Moshe Baru
Summary. Recombinant activated factor VII (rFVIIa) is an effective treatment of the haemophilia patient with inhibitors and acquired haemophilia. However, on account of its relatively short half‐life (HL), achieving therapeutic efficacy with FVIIa requires repeated injections. The development of a long‐acting FVIIa product would therefore be beneficial. The formulat...... hiện toàn bộ
Rationale for the use of high dose rFVIIa in a high‐titre inhibitor patient with haemophilia B during major orthopaedic proceduresHaemophilia - Tập 7 Số 5 - Trang 517-522 - 2001
Herbert Cooper, Connie P. Jones, Edmund Campion, Barbara A. Konkle, Ulla Hedner
Inhibitor development is a serious complication in patients with haemophilia A and B. Historically, a lack of optimal therapies and factor products for treating inhibitor patients resulted in many patients developing chronic haemophilic arthropathies and flexion contractures of the involved joints. The introduction of immune‐tolerance protocols to eradicate high‐titre inhibitors has greatl...... hiện toàn bộ
Results of a phase I/II open‐label, safety and efficacy trial of coagulation factor IX (recombinant), albumin fusion protein in haemophilia B patientsHaemophilia - Tập 21 Số 6 - Trang 784-790 - 2015
Uri Martinowitz, Toshko Lissitchkov, Aaron Lubetsky, Gantcho Jotov, Tami Brutman‐Barazani, C. Voigt, Iris Jacobs, T. Wuerfel, Elena Santagostino
IntroductionrIX‐FP is a coagulation factor IX (recombinant), albumin fusion protein with more than fivefold half‐life prolongation over other standard factor IX (FIX) products available on the market.AimThis prospective phase II, open‐label study evaluated the safety and efficacy of rIX‐FP for...... hiện toàn bộ
In silico calculated affinity of FVIII‐derived peptides for HLA class II alleles predicts inhibitor development in haemophilia A patients with missense mutations in the F8 geneHaemophilia - Tập 20 Số 2 - Trang 176-184 - 2014
Anastas Pashov, Thierry Calvez, Laurent Gilardin, Bernard Maillère, Yohann Repessé, Johannes Oldenburg, A. Pavlova, Srini V. Kaveri, Sébastien Lacroix‐Desmazes
SummaryForty per cent of haemophilia A (HA) patients have missense mutations in the F8 gene. Yet, all patients with identical mutations are not at the same risk of developing factor VIII (FVIII) inhibitors. In severe HA patients, human leucocy...... hiện toàn bộ
Safety procedures of coagulation factorsHaemophilia - Tập 13 Số s5 - Trang 41-46 - 2007
Juan I. Jorquera
Abstract Two main types of safety procedures must be applied to biological products, including plasma derivatives: (i) preventive procedures and (ii) elimination procedures.Prevention includes epidemiological control of donor populations; checks on each donor’s health condition; analysis of each donation for the main pathogens using serological methods; additional a...... hiện toàn bộ
Nanofiltration of plasma‐derived biopharmaceutical productsHaemophilia - Tập 9 Số 1 - Trang 24-37 - 2003
Thierry Burnouf, Mirjana Radosevich
Summary. This review presents the current status on the use and benefits of viral removal filtration systems – known as nanofiltration – in the manufacture of plasma‐derived coagulation factor concentrates and other biopharmaceutical products from human blood origin.Nanofiltration of plasma products has been implemented at a production scale in the e...... hiện toàn bộ