Strategies for targeted nonviral delivery of siRNAs in vivo
Tài liệu tham khảo
Kim, 2009, Overview of gene silencing by RNA interference, Curr. Protoc. Nucleic. Acid Chem., 11
Kim, 2008, RNAi mechanisms and applications, Biotechniques, 44, 613, 10.2144/000112792
de Fougerolles, 2007, Interfering with disease: a progress report on siRNA-based therapeutics, Nat. Rev. Drug Discov., 6, 443, 10.1038/nrd2310
Watanabe, 2008, Endogenous siRNAs from naturally formed dsRNAs regulate transcripts in mouse oocytes, Nature, 453, 539, 10.1038/nature06908
Babiarz, 2008, Mouse ES cells express endogenous shRNAs, siRNAs and other microprocessor-independent, Dicer-dependent small RNAs, Genes Dev., 22, 2773, 10.1101/gad.1705308
Castanotto, 2009, The promises and pitfalls of RNA-interference-based therapeutics, Nature, 457, 426, 10.1038/nature07758
Manjunath, 2006, Interfering antiviral immunity: application, subversion, hope?, Trends Immunol., 27, 328, 10.1016/j.it.2006.05.006
Check, 2005, A crucial test, Nat. Med., 11, 243, 10.1038/nm0305-243
DeVincenzo, 2008, Evaluation of the safety, tolerability and pharmacokinetics of ALN-RSV01, a novel RNAi antiviral therapeutic directed against respiratory syncytial virus (RSV), Antiviral Res., 77, 225, 10.1016/j.antiviral.2007.11.009
Chappelow, 2008, Neovascular age-related macular degeneration: potential therapies, Drugs, 68, 1029, 10.2165/00003495-200868080-00002
Kleinman, 2008, Sequence- and target-independent angiogenesis suppression by siRNA via TLR3, Nature, 452, 591, 10.1038/nature06765
Kirchhoff, 2008, Silencing HIV-1 in vivo, Cell, 134, 566, 10.1016/j.cell.2008.08.004
Grimm, 2007, Therapeutic application of RNAi: is mRNA targeting finally ready for prime time?, J. Clin. Invest., 117, 3633, 10.1172/JCI34129
Manjunath, N. et al. (2009) Lentiviral delivery of short hairpin RNAs. Adv Drug Deliv Rev. (in press)
Akhtar, 2007, Nonviral delivery of synthetic siRNAs in vivo, J. Clin. Invest., 117, 3623, 10.1172/JCI33494
Aagaard, 2007, RNAi therapeutics: principles, prospects and challenges, Adv. Drug Deliv. Rev., 59, 75, 10.1016/j.addr.2007.03.005
Detzer, 2008, Phosphorothioate-stimulated cellular uptake of siRNA: a cell culture model for mechanistic studies, Curr. Pharm. Des., 14, 3666, 10.2174/138161208786898770
Juliano, 2008, Mechanisms and strategies for effective delivery of antisense and siRNA oligonucleotides, Nucleic. Acids Res., 36, 4158, 10.1093/nar/gkn342
Dykxhoorn, 2006, The silent treatment: siRNAs as small molecule drugs, Gene Ther., 13, 541, 10.1038/sj.gt.3302703
Lewis, 2002, Efficient delivery of siRNA for inhibition of gene expression in postnatal mice, Nat. Genet, 32, 107, 10.1038/ng944
Rippe, 2002, Transendothelial transport: the vesicle controversy, J. Vasc. Res., 39, 375, 10.1159/000064521
Greish, 2007, Enhanced permeability and retention of macromolecular drugs in solid tumors: a royal gate for targeted anticancer nanomedicines, J. Drug Target., 15, 457, 10.1080/10611860701539584
Zamecnik, 2004, Extracellular matrix glycoproteins and diffusion barriers in human astrocytic tumors, Neuropathol. Appl. Neurobiol., 30, 338, 10.1046/j.0305-1846.2003.00541.x
Oliveira, 2007, Fusogenic peptides enhance endosomal escape improving siRNA-induced silencing of oncogenes, Int. J. Pharm., 331, 211, 10.1016/j.ijpharm.2006.11.050
Song, 2003, RNA interference targeting Fas protects mice from fulminant hepatitis, Nat. Med., 9, 347, 10.1038/nm828
Fattal, 2008, State of the art and perspectives for the delivery of antisense oligonucleotides and siRNA by polymeric nanocarriers, Int. J. Pharm., 364, 237, 10.1016/j.ijpharm.2008.06.011
Hornung, 2005, Sequence-specific potent induction of IFN-alpha by short interfering RNA in plasmacytoid dendritic cells through TLR7, Nat. Med., 11, 263, 10.1038/nm1191
Kim, 2007, Strategies for silencing human disease using RNA interference, Nat. Rev. Genet., 8, 173, 10.1038/nrg2006
Liu, 2007, Exploring cell type-specific internalizing antibodies for targeted delivery of siRNA, Brief Funct. Genomic Proteomic, 6, 112, 10.1093/bfgp/elm015
Chiu, 2004, Visualizing a correlation between siRNA localization, cellular uptake and RNAi in living cells, Chem. Biol., 11, 1165, 10.1016/j.chembiol.2004.06.006
Rossi, 2005, Receptor-targeted siRNAs, Nat. Biotechnol., 23, 682, 10.1038/nbt0605-682
Urban-Klein, 2005, RNAi-mediated gene-targeting through systemic application of polyethylenimine (PEI)-complexed siRNA in vivo, Gene Ther., 12, 461, 10.1038/sj.gt.3302425
Kumar, 2007, Transvascular delivery of small interfering RNA to the central nervous system, Nature, 448, 39, 10.1038/nature05901
Kumar, 2008, T cell-specific siRNA delivery suppresses HIV-1 infection in humanized mice, Cell, 134, 577, 10.1016/j.cell.2008.06.034
Zimmermann, 2006, RNAi-mediated gene silencing in non-human primates, Nature, 441, 111, 10.1038/nature04688
Kawakami, 2007, Targeted delivery systems of small interfering RNA by systemic administration, Drug Metab. Pharmacokinet., 22, 142, 10.2133/dmpk.22.142
Jeong, 2009, siRNA conjugate delivery systems, Bioconjug. Chem., 20, 5, 10.1021/bc800278e
Soutschek, 2004, Therapeutic silencing of an endogenous gene by systemic administration of modified siRNAs, Nature, 432, 173, 10.1038/nature03121
Peer, 2008, Systemic leukocyte-directed siRNA delivery revealing cyclin D1 as an anti-inflammatory target, Science, 319, 627, 10.1126/science.1149859
Tompkins, 2004, Protection against lethal influenza virus challenge by RNA interference in vivo, Proc. Natl. Acad. Sci. U S A, 101, 8682, 10.1073/pnas.0402630101
Palliser, 2006, An siRNA-based microbicide protects mice from lethal herpes simplex virus 2 infection, Nature, 439, 89, 10.1038/nature04263
Kumar, 2006, A single siRNA suppresses fatal encephalitis induced by two different flaviviruses, PLoS Med., 3, e96, 10.1371/journal.pmed.0030096
Pardridge, 2007, shRNA and siRNA delivery to the brain, Adv. Drug Deliv. Rev., 59, 141, 10.1016/j.addr.2007.03.008
Zhang, 2004, Intravenous RNA interference gene therapy targeting the human epidermal growth factor receptor prolongs survival in intracranial brain cancer, Clin. Cancer Res., 10, 3667, 10.1158/1078-0432.CCR-03-0740
Pirollo, 2006, Tumor-targeting nanoimmunoliposome complex for short interfering RNA delivery, Hum. Gene. Ther., 17, 117, 10.1089/hum.2006.17.117
Hogrefe, 2006, Chemically modified short interfering hybrids (siHYBRIDS): nanoimmunoliposome delivery in vitro and in vivo for RNAi of HER-2, Nucleosides Nucleotides Nucleic. Acids, 25, 889, 10.1080/15257770600793885
Morrissey, 2005, Potent and persistent in vivo anti-HBV activity of chemically modified siRNAs, Nat. Biotechnol., 23, 1002, 10.1038/nbt1122
Ma, 2005, Cationic lipids enhance siRNA-mediated interferon response in mice, Biochem. Biophys. Res. Commun., 330, 755, 10.1016/j.bbrc.2005.03.041
Akinc, 2008, A combinatorial library of lipid-like materials for delivery of RNAi therapeutics, Nat. Biotechnol., 26, 561, 10.1038/nbt1402
Shim, 2008, Controlled delivery of plasmid DNA and siRNA to intracellular targets using ketalized polyethylenimine, Biomacromolecules, 9, 444, 10.1021/bm7007313
Tan, 2005, Gene knockdown with intrathecal siRNA of NMDA receptor NR2B subunit reduces formalin-induced nociception in the rat, Gene. Ther., 12, 59, 10.1038/sj.gt.3302376
Thomas, 2005, Full deacylation of polyethylenimine dramatically boosts its gene delivery efficiency and specificity to mouse lung, Proc. Natl. Acad Sci. U S A, 102, 5679, 10.1073/pnas.0502067102
Chiu, 2004, Tumor-targeted gene delivery via anti-HER2 antibody (trastuzumab, Herceptin) conjugated polyethylenimine, J. Control Release, 97, 357, 10.1016/j.jconrel.2004.03.019
Kim, 2006, Comparative evaluation of target-specific GFP gene silencing efficiencies for antisense ODN, synthetic siRNA and siRNA plasmid complexed with PEI-PEG-FOL conjugate, Bioconjug. Chem., 17, 241, 10.1021/bc050289f
Guo, 2006, Construction of folate-conjugated pRNA of bacteriophage phi29 DNA packaging motor for delivery of chimeric siRNA to nasopharyngeal carcinoma cells, Gene. Ther., 13, 814, 10.1038/sj.gt.3302856
Pirollo, 2007, Materializing the potential of small interfering RNA via a tumor-targeting nanodelivery system, Cancer Res., 67, 2938, 10.1158/0008-5472.CAN-06-4535
Park, 2002, Anti-HER2 immunoliposomes: enhanced efficacy attributable to targeted delivery, Clin. Cancer Res., 8, 1172
Mamot, 2005, Epidermal growth factor receptor-targeted immunoliposomes significantly enhance the efficacy of multiple anticancer drugs in vivo, Cancer Res., 65, 11631, 10.1158/0008-5472.CAN-05-1093
Schiffelers, 2004, Cancer siRNA therapy by tumor selective delivery with ligand-targeted sterically stabilized nanoparticle, Nucleic. Acids Res., 32, e149, 10.1093/nar/gnh140
Alshamsan, 2009, Formulation and delivery of siRNA by oleic acid and stearic acid modified polyethylenimine, Mol. Pharm., 6, 121, 10.1021/mp8000815
Zintchenko, 2008, Simple modifications of branched PEI lead to highly efficient siRNA carriers with low toxicity, Bioconjug. Chem., 19, 1448, 10.1021/bc800065f
Howard, 2009, Chitosan/siRNA nanoparticle-mediated TNF-alpha knockdown in peritoneal macrophages for anti-inflammatory treatment in a murine arthritis model, Mol. Ther., 17, 162, 10.1038/mt.2008.220
Howard, 2006, RNA interference in vitro and in vivo using a novel chitosan/siRNA nanoparticle system, Mol. Ther., 14, 476, 10.1016/j.ymthe.2006.04.010
Zhang, 2005, Inhibition of respiratory syncytial virus infection with intranasal siRNA nanoparticles targeting the viral NS1 gene, Nat. Med., 11, 56, 10.1038/nm1174
Hu-Lieskovan, 2005, Sequence-specific knockdown of EWS-FLI1 by targeted, nonviral delivery of small interfering RNA inhibits tumor growth in a murine model of metastatic Ewing's sarcoma, Cancer Res., 65, 8984, 10.1158/0008-5472.CAN-05-0565
Aouadi, 2009, Orally delivered siRNA targeting macrophage Map4k4 suppresses systemic inflammation, Nature, 458, 1180, 10.1038/nature07774
Vangasseri, 2005, Lipid-protamine-DNA-mediated antigen delivery, Curr. Drug Deliv., 2, 401, 10.2174/156720105774370168
Song, 2005, Antibody mediated in vivo delivery of small interfering RNAs via cell surface receptors, Nat. Biotechnol., 23, 709, 10.1038/nbt1101
Peer, 2007, Selective gene silencing in activated leukocytes by targeting siRNAs to the integrin lymphocyte function-associated antigen-1, Proc. Natl. Acad Sci. U S A, 104, 4095, 10.1073/pnas.0608491104
Schwarze, 1999, In vivo protein transduction: delivery of a biologically active protein into the mouse, Science, 285, 1569, 10.1126/science.285.5433.1569
Torchilin, 2001, TAT peptide on the surface of liposomes affords their efficient intracellular delivery even at low temperature and in the presence of metabolic inhibitors, Proc. Natl. Acad Sci. U S A, 98, 8786, 10.1073/pnas.151247498
Kim, 2006, Cholesteryl oligoarginine delivering vascular endothelial growth factor siRNA effectively inhibits tumor growth in colon adenocarcinoma, Mol. Ther., 14, 343, 10.1016/j.ymthe.2006.03.022
McNamara, 2006, Cell type-specific delivery of siRNAs with aptamer-siRNA chimeras, Nat. Biotechnol., 24, 1005, 10.1038/nbt1223
Chu, 2006, Aptamer mediated siRNA delivery, Nucleic. Acids Res., 34, e73, 10.1093/nar/gkl388
Zhou, 2008, Novel dual inhibitory function aptamer-siRNA delivery system for HIV-1 therapy, Mol. Ther., 16, 1481, 10.1038/mt.2008.92
Zhou, 2009, Selection, characterization and application of new RNA HIV gp120 aptamers for facile delivery of Dicer substrate siRNAs into HIV infected cells, Nucleic. Acids Res., 37, 3094, 10.1093/nar/gkp185
Marshall, 2003, Gene therapy. Second child in French trial is found to have leukemia, Science, 299, 320, 10.1126/science.299.5605.320
Hacein-Bey-Abina, 2002, Gene therapy of X-linked severe combined immunodeficiency, Int. J. Hematol., 76, 295, 10.1007/BF02982686
Song, 2003, Sustained small interfering RNA-mediated human immunodeficiency virus type 1 inhibition in primary macrophages, J. Virol., 77, 7174, 10.1128/JVI.77.13.7174-7181.2003
Omi, 2004, Long-lasting RNAi activity in mammalian neurons, FEBS Lett., 558, 89, 10.1016/S0014-5793(04)00017-1
Cardoso, 2008, Tf-lipoplexes for neuronal siRNA delivery: a promising system to mediate gene silencing in the CNS, J. Control Release, 132, 113, 10.1016/j.jconrel.2008.08.014