Steroids in duchenne muscular dystrophy — Deflazacort trial

Hoffman, 1987, Dystrophin: the protein product of the Duchenne muscular dystrophy locus, Cell, 51, 919, 10.1016/0092-8674(87)90579-4

Koenig, 1987, Complete cloning of the Duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals, Cell, 50, 509, 10.1016/0092-8674(87)90504-6

Zubrzycka-Gaarn, 1988, The Duchenne muscular dystrophy gene product is localized in the sarcolemma of human skeletal muscle fibers, Nature, 333, 466, 10.1038/333466a0

Drachman, 1974, Prednisone in Duchenne muscular dystrophy, Lancet, 2, 1409, 10.1016/S0140-6736(74)90071-3

Siegel, 1974, Failure of corticosteroid in the treatment of Duchenne (pseudo hypertrophic) muscular dystrophy: report of a clinically age matched three year double-blind suty, Int Med J, 145, 32

De Silva, 1987, Prednisone treatment in Duchenne muscular dystrophy. Long term benefit, Arch Neurol, 44, 818, 10.1001/archneur.1987.00520200022012

Brooke, 1987, Clinical investigation of Duchenne muscular dystrophy. Interesting results in a trial of prednisone, Arch Neurol, 44, 812, 10.1001/archneur.1987.00520200016010

Mendell, 1989, Randomized double blind trial of prednisone in Duchenne's muscular dystrophy, N Eng J Med, 320, 1592, 10.1056/NEJM198906153202405

Griggs, 1990, Prednisone in Duchenne dystrophy. A randomized, controlled trial defining the time course and dose response, Arch Neurol, 48, 383, 10.1001/archneur.1991.00530160047012

Nathanson, 1987, Steroid possessing nitrogen atoms. III. Synthesis of new highly active corticoids [17-d]oxazolino steroids, J Med Chem, 10, 799, 10.1021/jm00317a009

Nathanson, 1969, Steroid possessing nitrogen atoms. IV. Further studies on the synthesis of [17, 16-]oxazolino steroids, Steroids, 13, 383, 10.1016/0039-128X(69)90046-4

Avioli, 1986

De Rosa, 1990, Deflazacort in myastenia gravis, J Neurol Sci, 98, 417

Brooke, 1981, Clinical trial in Duchenne dystrophy. I The design of the protocol, Muscle Nerve, 4, 186, 10.1002/mus.880040304

Scott, 1982, Quantitation of muscle function in children: a prospective study in Duchenne muscular dystrophy, Muscle Nerve, 5, 291, 10.1002/mus.880050405

Rowland, 1975, Prednisone in Duchenne dystrophy, Lancet, 1, 277

Griggs, 1990, Randomized, double blind trial of mazindol in Duchenne dystrophy, Muscle Nerve, 13, 1169, 10.1002/mus.880131212

Edwards, 1984, Weight reduction in boys with muscular dystrophy, Dev Med Child Neurol, 26, 384, 10.1111/j.1469-8749.1984.tb04457.x

Griffiths, 1988, A new chart for weight control in Duchenne muscular dystrophy, Arch Dis Child, 63, 1256, 10.1136/adc.63.10.1256