Ramucirumab as second-line treatment in patients with advanced hepatocellular carcinoma: Japanese subgroup analysis of the REACH trial

Gastroenterologia Japonica - Tập 52 - Trang 494-503 - 2016
Masatoshi Kudo1, Etsuro Hatano2, Shinichi Ohkawa3, Hirofumi Fujii4, Akihide Masumoto5, Junji Furuse6, Yoshiyuki Wada7, Hiroshi Ishii8, Shuntaro Obi9, Shuichi Kaneko10, Seiji Kawazoe11, Osamu Yokosuka12, Masafumi Ikeda13, Katsuaki Ukai14, Sojiro Morita15, Akihito Tsuji16, Toshihiro Kudo17, Mitsuo Shimada18, Yukio Osaki19, Ryosuke Tateishi20, Gen Sugiyama21, Paolo Benjamin Abada22, Ling Yang23, Takuji Okusaka24, Andrew Xiuxuan Zhu
1Kindai University Faculty of Medicine, Osaka-Sayama, Japan
2Kyoto University Hospital, Kyoto, Japan
3Kanagawa Cancer Center, Yokohama, Japan
4Jichi Medical University, Shimotsuke, Japan
5Aso Iizuka Hospital, Fukuoka, Japan
6Kyorin University School of Medicine Hospital, Tokyo, Japan
7National Hospital Organization Kyushu Medical Center, Fukuoka, Japan
8The Cancer Institute Hospital of the Japanese Foundation for Cancer Research, Tokyo, Japan
9Kyoundo Hospital, Sasaki Institute, Tokyo, Japan
10Kanazawa University Hospital, Ishikawa, Japan
11SAGA-KEN MEDICAL CENTRE KOSEIKAN, Saga, Japan
12Chiba University Hospital, Chiba, Japan
13National Cancer Center Hospital East, Chiba, Japan
14Sendai Medical Center, Sendai, Japan
15Kochi Health Sciences Center, Kochi, Japan
16Kagawa University Hospital, Takamatsu, Japan
17Osaka University Hospital, Osaka, Japan
18Tokushima University Hospital, Tokushima, Japan
19Osaka Red Cross Hospital, Osaka, Japan
20The University of Tokyo Hospital, Tokyo, Japan
21Kurume University Medical Center, Fukuoka, Japan
22Eli Lilly and Company, Indianapolis, USA
23Eli Lilly and Company, Bridgewater, USA
24National Cancer Center Hospital, Tokyo, Japan

Tóm tắt

REACH evaluated ramucirumab in the second-line treatment of patients with advanced hepatocellular carcinoma. In the intent-to-treat population (n = 565), a significant improvement in overall survival (OS) was not observed. In patients with an elevated baseline α-fetoprotein (AFP) level (400 ng/mL or greater), an improvement in OS was demonstrated. An analysis of the Japanese patients in REACH was performed. An analysis was performed with the subset of the intent-to-treat population enrolled in Japan (n = 93). The median OS was 12.9 months for the ramucirumab arm (n = 45) and 8.0 months for the placebo arm (n = 48) [hazard ratio (HR) 0.621 (95 % confidence interval (CI) 0.391–0.986); P = 0.0416]. The median progression-free survival was 4.1 months for the ramucirumab arm and 1.7 months for the placebo arm [HR 0.449 (95 % CI 0.285–0.706); P = 0.0004]. The objective response rates were 11 % for the ramucirumab arm and 2 % for the placebo arm (P = 0.0817). The grade 3 or higher treatment-emergent adverse events occurring in more than 5 % of patients with a higher incidence for the ramucirumab arm (n = 44) than for the placebo arm (n = 47) were ascites (7% vs 2 %), hypertension (7 % vs 2 %), and cholangitis (7 % vs 0 %). In patients with a baseline AFP level of 400 ng/mL or greater, the median OS was 12.9 months for the ramucirumab arm (n = 20) and 4.3 months for the placebo arm (n = 22) [HR 0.464 (95 % CI 0.232–0.926); P = 0.0263]. In the Japanese patients in REACH, ramucirumab treatment improved OS, including in patients with a baseline AFP level of 400 ng/mL or greater; improvements in progression-free survival and objective response rate were also demonstrated. The safety profile of ramucirumab was acceptable and well tolerated in Japanese patients. ClinicalTrials.gov identifier NCT01140347.

Tài liệu tham khảo

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