Predictive factors of renal toxicities related to anti-VEGFR multikinase inhibitors in phase 1 trials

Investigational New Drugs - Tập 35 - Trang 79-86 - 2016
Emilie Boissier1, Olivier Mir1, Antoine Hollebecque1, Hassan Izzedine2, Stéphane Ederhy3, Anas Gazzah1, Rastislav Bahleda1, Christophe Massard1, Isabelle Macquin-Mavier4, Christophe Tournigand5,6, Jean-Philippe Spano7,8, Jean-Charles Soria1,9, Benoît Rousseau4,5,6,10,11
1Department of Drug Development (DITEP), Gustave Roussy Institute, Villejuif, France
2Department of Nephrology, Park Monceau International Clinic, Paris, France
3Department of Cardiology, Saint Antoine Teaching Hospital, Paris, France
4Clinical Pharmacology, Henri Mondor Teaching Hospital, Créteil, France
5Faculty of Medicine, University of Paris-Est, Créteil, France
6Department of Medical Oncology, Henri Mondor Teaching Hospital, Assistance Publique – Hôpitaux de Paris, Créteil, France
7Department of Medical Oncology, Pitié Salpêtrière Teaching Hospital, Paris, France
8Faculty of Medicine, Université Pierre et Marie Curie, Paris, France
9Faculty of Medicine, Paris Sud University, Le Kremlin-Bicêtre, France
10INSERM U955 Team 18, Créteil Cedex, France
11Oncologie médicale, CHU Henri Mondor, Créteil, France

Tóm tắt

Purpose Renal toxicities are common with angiogenesis multikinase inhibitors (AMKI), and can be limiting in phase I trials. Factors associated with such toxicities are poorly known. The aims of this exploratory study were to describe renovascular toxicities associated with AMKI, impact on drug development and to identify baseline parameters associated with the occurrence of renal toxicities in phase I trials. Methods Consecutive patients treated with AMKI in Gustave Roussy phase I unit between October 2005 and August 2013 were included. We retrospectively collected baseline characteristics and renovascular side effects. Associations were assessed in univariate and multivariate analyses. Results Overall, 168 patients were included: male 53.0 %, mean age 55.5 years old, history of hypertension 26.8 %, diabetes 6.0 %, atherosclerosis 13.6 %, stage 3 Chronic Kidney Disease (CKD, NKF-KDOQI) 17.2 %. Incidences of reno-vascular side effects were: hypertension 47.6 %, proteinuria 19.0 %, renal failure 11.9 % and thrombotic microangiopathy 10.1 %. Eighty percent of dose limiting toxicities (DLTs) were related to a renal toxicity. Multivariate analysis showed that onset of renal failure was associated with history of hypertension (p = 0.0003) and stage 3 CKD (p = 0.032). Conclusions A majority of the DLTs associated with AMKI in phase 1 trials are renal toxicities. Baseline hypertension and stage 3 CKD (NKF-KDOQI) might help to better identify patients at risk of AMKI-related renal toxicities.

Tài liệu tham khảo

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