Phase I clinical and pharmacokinetic study of orally administeredN 4-palmitoyl-1-β-d-arabinofuranosylcytosine

Springer Science and Business Media LLC - Tập 4 - Trang 67-73 - 1987
Ryuzo Ohno1, Kiyoji Kimura2, Kazuo Ota3, Yasusada Miura4, Akira Hoshino5, Kenichi Hattori6, Masami Hirano7, Munemoto Ito8, Tadashi Maekawa9, Toru Nakamura10, Ikuo Kimura11, Michito Ichimaru12, Yoshiro Uzuka13, Masao Oguro14, Tamotsu Miyazaki15, Yasunobu Sakai16, Yutaka Hirota2, Ichita Amaki17, Shigeyuki Osamura18, Toru Masaoka19, Fumimaro Takaku20, Kazumasa Yamada21
1First Department of Internal Medicine, Nagoya University School of Medicine, Nagoya, Japan
2National Nagoya Hospital, Nagoya
3Aichi Cancer Center, Nagoya
4Jichi Medical School, Minami Kawachi
5Anjo Kosei Hospital, Anjo
6Kanazawa University School of Medicine, Kanazawa
7Fujita Gakuen University School of Medicine, Toyoake
8National Tokyo Second Hospital, Tokyo
9Gunma University School of Medicine, Maebashi
10Fukui Medical School, Fukui
11Okayama University School of Medicine, Okayama
12Nagasaki University School of Medicine, Nagasaki
13Tohoku University School of Medicine, Sendai
14Chiba Cancer Center, Chiba
15Hokkaido University School of Medicine, Sapporo
16Komagome Municipal Hospital, Tokyo
17Nihon University School of Medicine, Tokyo
18Tokyo Medical College, Tokyo
19Center for Adult Diseases, Osaka
20Tokyo University Faculty of Medicine, Tokyo
21Nagoya University Branch Hospital, Nagoya

Tóm tắt

A phase I study ofN 4-palmitoyl-1-β-d-arabinofuranosylcytosine (PLAC) was conducted in 88 patients; 36 with solid tumors and 52 with hematological malignancies, using 2 different schedules. Schedule 1 employed a single oral administration and Schedule 2, 5-day consecutive daily oral administration. In Schedule 1, the daily dose was initiated with 1 mg kg−1 which was escalated up to 24 mg kg−1 according to the modified Fibonacci’s method. Side effects included nausea, vomiting and skin rashes, but myelosuppression was not seen within this dose range. In Schedule 2, the daily dose was started with 1 mg kg−1 which was escalated up to 24 mg kg−1. Major side effects were nausea, vomiting and amorexia, and mild myelosuppression was noted at 12 mg kg−1 or more. The dose-limiting toxicity was gastrointestinal toxicity, which appeared at 3.3 mg kg−1 or more and became frequent at 7 mg kg−1 or more. Pharmacokinetic study revealed that the plasma concentrations of PLAC and ara-C, obtained by the oral intake of 3.3 mg kg−1 or more of PLAC, were sufficient for these compounds to exert cytotoxic effects on various human leukemia cellsin vitro. Based on these observations and plausible mechanism of action of PLAC, further clinical study should be carried out in a treatment schedule of considerably prolonged administration period with 3.3–6 mg kg−1 day−1 of PLAC.

Tài liệu tham khảo

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