Nusinersen does not improve lung function in a cohort of children with spinal muscular atrophy – A single-center retrospective study

European Journal of Paediatric Neurology - Tập 31 - Trang 88-91 - 2021
Laura Heitschmidt1, Leopold Pichlmaier1, Maximilian Eckerland1, Mathis Steindor1, Margarete Olivier1, Ina Fuge1, Heike Kölbel2, Raphael Hirtz3, Florian Stehling1
1Department of Pediatric Pulmonology and Sleep Medicine, Children's Hospital, University of Duisburg-Essen, Essen, Germany
2Department of Pediatric Neurology, Children's Hospital, University of Duisburg-Essen, Essen, Germany
3Department of Pediatric Endocrinology, Children's Hospital, University of Duisburg-Essen, Essen, Germany

Tài liệu tham khảo

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