Manipulating proteostasis to repair the F508del-CFTR defect in cystic fibrosis

Speranza Esposito1, Antonella Tosco2, Valeria Rachela Villella1, Valeria Raia2, Guido Kroemer3,4,5,6, Luigi Maiuri1,7
1Division of Genetics and Cell Biology (Italy)
2Department of Pediatrics, Regional Cystic Fibrosis Center (Naples - Italy)
3Department of Women's and Children's Health (Q2:07, Stockholm, SE 171 76 - Sweden)
4Equipe labellisée Ligue contre le cancer - CRC - Inserm U1138 - Apoptose, cancer et immunité (Site 1 : Gustave Roussy,114 rue Édouard-Vaillant, 94805 Villejuif Cedex- France - Site 2 : Centre de Recherche des Cordeliers, 15 rue de l'Ecole de Médecine, 75006 Paris- France - France)
5Plateforme de métabolomique (Gustave Roussy - France)
6UPMC - Université Pierre et Marie Curie - Paris 6 (4 place Jussieu - 75005 Paris - France)
7SCDU of Pediatrics (Italy)

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