Management and monitoring recommendations for the use of eliglustat in adults with type 1 Gaucher disease in Europe

European Journal of Internal Medicine - Tập 37 - Trang 25-32 - 2017
Nadia Belmatoug1, Maja Di Rocco2, Cristina Fraga3, Pilar Giraldo4, Derralynn Hughes5, Elena Lukina6, Pierre Maison-Blanche7, Martin Merkel8, Claus Niederau9, Ursula Plӧckinger10, Johan Richter11, Thomas M. Stulnig12, Stephan vom Dahl13, Timothy M. Cox14
1Referral Center for Lysosomal Diseases, University Beaujon Hospital Paris Nord Val de Seine, Assistance-Publique Hôpitaux de Paris, Department of Internal Medicine, 100 Boulevard du Général Leclerc, 92110 Clichy, France
2Unit of Rare Diseases, Department Pediatrics, Gaslini Institute, Largo Gaslini 3, 16147 Genoa, Italy
3Department of Haematology, HDES Hospital, Ponta Delgada, Av. D. Manuel I, PDL, Açores, Portugal
4Translational Research Unit, Instituto Investigación Sanitaria Aragon, CIBER Enfermedades Raras (CIBERER), Zaragoza, Spain
5Royal Free London NHS Foundation Trust, University College London, Department of Haematology, Pond St., London NW1 2QG, United Kingdom
6Department of Orphan Diseases, Hematology Research Center, 4 Novy Zykovsky Lane, 125167 Moscow, Russia
7Bichat University Hospital, Cardiology Unit, 46 Rue Henri Huchard, 75018 Paris, France
8Department of Internal Medicine, Asklepios Klinik St. Georg, Lohmühlenstr. 5, 20099 Hamburg, Germany
9Katholisches Klinikum Oberhausen GmbH, St. Josef Hospital, Department of Medicine, Academic Teaching Hospital, Universität Duisburg-Essen, Mülheimer Str. 83, 46045 Oberhausen, Germany
10Interdisziplinares Stoffwechsel-Centrum: Diabetes, Endokrinologie und Stoffwechsel, Charité Universitätsmedizin Berlin, Campus Virchow-Klinikum, Augustenburger Platz 1, 13352 Berlin, Germany
11Department of Hematology and Vascular Diseases, Skåne University Hospital, 221 85 Lund, Sweden
12Clinical Division of Endocrinology and Metabolism, Department of Medicine III, Medical University of Vienna, Waehringer Guertel 18-20, 1090 Vienna, Austria
13Department of Gastroenterology, Hepatology and Infectious Diseases, University Hospital, University of Duesseldorf, Moorenstrasse 5, D-40225, Germany
14Department of Medicine, University of Cambridge, Box 157, Level 5, Addenbrooke's Hospital, Cambridge CB2 0QQ, United Kingdom

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European Journal of Internal Medicine

Tập 37

25-32

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