Amit Nathwani1,2,3, Ulreke M. Reiss4, Graham Davies1,2, Cecilia Rosales1,3, Pratima Chowdary2, Jenny McIntosh1,2, Marco Della Peruta1, Elsa Lhériteau1, Nishal Patel1, Deepak B. Thimiri Govinda Raj1,3, Anne Riddell2, Jun Pie2, Savita Rangarajan5,6, David Bevan6, Michael Recht7, Yu‐Min Shen8, Kathleen G. Halka9, Etiena Basner‐Tschakarjan10, Nicole K. Paulk10, Katherine A. High10, James A. Allay11, Mark A. Kay12, Catherine Y. Ng13, Junfang Zhou13, Maria Cancio13, Christopher L. Morton13, John T. Gray4, Deo Kumar Srivastava14, Arthur W. Nienhuis4, Andrew M. Davidoff13
1Department of Haematology, University College London Cancer Institute;
2Katharine Dormandy Haemophilia Centre and Thrombosis Unit, Royal Free NHS Trust
3London, NHS Blood and Transplant, Watford
4Departments of Hematology, Memphis, TN
5Basingstoke and North Hampshire Foundation Trust, Basingstoke
6St Thomas' Hospital
7Hemophilia Center, Oregon Health and Science University, Portland
8Department of Internal Medicine, University of Texas Southwestern Medical Center, Dallas.
9Scott and White Healthcare, Temple Clinic, Temple
10Center for Cellular and Molecular Therapeutics, Children's Hospital of Philadelphia, Philadelphia
11St. Jude Children's Research Hospital, and Poplar Healthcare, Memphis, TN
12Departments of Pediatrics and Genetics, Stanford University School of Medicine, Palo Alto, CA
13Surgery, Memphis, TN
14Biostatistics, Memphis, TN
