Sử dụng dịch vụ y tế và nhu cầu chưa được đáp ứng của bệnh nhân mắc hội chứng kháng tổng hợp: Một cuộc khảo sát quốc tế về bệnh nhân

Springer Science and Business Media LLC - Tập 43 - Trang 1925-1934 - 2023
M. Weiss1,2, M. T. Holzer3, F. Muehlensiepen4, Y. Ignatyev4, C. Fiehn5, J. Bauhammer5, J. Schmidt6,7,8, S. Schlüter9, A. Dihkan10, D. Scheibner9, U. Schneider11, L. Valor-Mendez1,2, G. Corte1,2, L. Gupta12,13,14, H. Chinoy15,16, I. Lundberg17,18, L. Cavagna19, J. H. W. Distler1,2, G. Schett1,2, J. Knitza1,2
1Department of Internal Medicine 3, Friedrich-Alexander-University Erlangen-Nürnberg and Universitätsklinikum Erlangen, Erlangen, Germany
2Deutsches Zentrum Immuntherapie (DZI), Friedrich-Alexander-University, Erlangen, Germany
3III. Department of Internal Medicine, University Medical Center Hamburg-Eppendorf, Hamburg, Germany
4Faculty of Health Sciences, Center for Health Services Research, Brandenburg Medical School Theodor Fontane, Rüdersdorf, Germany
5Praxis für Rheumatologie, Klinische Immunologie, Medical Center, Baden-Baden, Germany
6Faculty of Health Sciences Brandenburg, Brandenburg Medical School Theodor Fontane, Rüdersdorf bei Berlin, Germany
7Department of Neurology and Pain Treatment, Center for Translational Medicine, Neuromuscular Center, Immanuel Klinik Rüdersdorf, University Hospital of the Brandenburg Medical School Theodor Fontane, Rüdersdorf bei Berlin, Germany
8Department of Neurology, Neuromuscular Center, University Medical Center, Göttingen, Germany
9Myositis-Gruppe, Deutsche Gesellschaft Für Muskelkranke, Freiburg, Germany
10The Swedish Working Group for Myositis, The Swedish Rheumatism Association, Stockholm, Sweden
11Department of Rheumatology, Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany
12Department of Rheumatology, Royal Wolverhampton Hospitals NHS Trust, Wolverhampton, UK
13Division of Musculoskeletal and Dermatological Sciences, School of Biological Sciences, Centre for Musculoskeletal Research, The University of Manchester, Manchester, UK
14Department of Rheumatology, City Hospital, Sandwell and West Birmingham Hospitals NHS Trust, Birmingham, UK
15Department of Rheumatology, Salford Royal Hospital, Northern Care Alliance NHS Foundation Trust, Manchester Academic Health Science Centre, Salford, UK
16Division of Musculoskeletal and Dermatological Sciences, Faculty of Biology, Medicine and Health, The University of Manchester, Manchester, UK
17Division of Rheumatology, Department of Medicine, Karolinska Institutet, Karolinska University Hospital, Solna, Sweden
18Department of Gastroenterology, Dermatology and Rheumatology, Karolinska University Hospital, Stockholm, Sweden
19Rheumatology Division, Fondazione Istituti di Ricovero e Cura a Carattere Scientifico (IRCCS) Policlinico San Matteo, Pavia, Italy

Tóm tắt

Hội chứng kháng tổng hợp (ASSD) là một căn bệnh tự miễn hiếm gặp, phức tạp và chưa được nghiên cứu nhiều. Các nghiên cứu dựa trên internet có thể vượt qua rào cản của nghiên cứu truyền thống tại chỗ và do đó rất hấp dẫn cho các bệnh hiếm. Mục tiêu của nghiên cứu này là điều tra các triệu chứng do bệnh nhân báo cáo, độ trễ chẩn đoán, tình trạng sức khỏe, tình trạng làm việc, kiến thức về bệnh tật và sự sẵn lòng tham gia vào nghiên cứu của bệnh nhân ASSD thông qua việc tiến hành một cuộc khảo sát quốc tế trực tuyến. Bảng câu hỏi đa ngôn ngữ đã được tạo ra bởi một nhóm bác sĩ chuyên khoa khớp và bệnh nhân quốc tế và được phân phối trực tuyến. 236 người tham gia từ 22 quốc gia đã hoàn thành khảo sát. 184/236 (78,0%) là nữ giới, độ tuổi trung bình (SD) là 49,6 năm (11,3) và kháng thể kháng tổng hợp phổ biến nhất là Jo-1 (169/236, 71,6%). 79/236 (33,5%) báo cáo làm việc toàn thời gian. Thời gian chẩn đoán trung vị là một năm. Triệu chứng phổ biến nhất khi khởi phát bệnh là mệt mỏi 159/236 (67,4%), tiếp theo là đau cơ 130/236 (55,1%). Bộ ba triệu chứng hoàn chỉnh của viêm cơ, viêm khớp và tổn thương phổi được xác nhận bởi bác sĩ là có ở 42/236 (17,8%) khi khởi phát bệnh và 88/236 (37,3%) trong quá trình bệnh. 36/236 (15,3%) báo cáo đã được chẩn đoán mắc bệnh fibromyalgia và 40/236 (16,3%) có trầm cảm. Các phương pháp điều trị ức chế miễn dịch được báo cáo nhiều nhất là corticosteroid đường uống 179/236 (75,9%), tiếp theo là rituximab 85/236 (36,0%). 73/236 (30,9%) đã nhận được điều trị vật lý trị liệu. 71/236 (30,1%) báo cáo biết các nguồn thông tin trực tuyến hữu ích liên quan đến ASSD. 223/236 (94,5%) sẵn lòng chia sẻ dữ liệu sức khỏe cho mục đích nghiên cứu một lần mỗi năm. Kết quả của chúng tôi nhấn mạnh rằng nghiên cứu dựa trên internet là vô giá trong việc hợp tác với bệnh nhân để thúc đẩy kiến thức về các bệnh hiếm gặp.

Từ khóa

#Hội chứng kháng tổng hợp #bệnh tự miễn #nghiên cứu dựa trên internet #khảo sát bệnh nhân #triệu chứng bệnh #chẩn đoán chậm

Tài liệu tham khảo

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