Generation of homozygous CRISPRa human induced pluripotent stem cell (hiPSC) lines for sustained endogenous gene activation
Tóm tắt
Từ khóa
Tài liệu tham khảo
Kemaladewi, 2019, A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene, Nature, 572, 125, 10.1038/s41586-019-1430-x
Schoger, 2020, CRISPR-Mediated Activation of Endogenous Gene Expression in the Postnatal Heart, Circ Res, 126, 6, 10.1161/CIRCRESAHA.118.314522
Min, 2019, CRISPR Correction of Duchenne Muscular Dystrophy, Annu. Rev. Med., 70, 239, 10.1146/annurev-med-081117-010451
Zhan, 2019, CRISPR/Cas9 for cancer research and therapy, Seminars in Cancer Biology, 55, 106, 10.1016/j.semcancer.2018.04.001