CD45 fraction bone marrow cells as potential delivery vehicles for genetically corrected dystrophin loci

Neuromuscular Disorders - Tập 12 - Trang S61-S66 - 2002
R.M.I Kapsa1,2, S.H.A Wong1,2, I Bertoncello3, A.F Quigley1,2, B Williams3, K Sells3, R Marotta1,2, M Kita1,2, P Simmons3, E Byrne1,2,4, A.J Kornberg1,2
1Melbourne Neuromuscular Research Institute, Clinical Neurosciences, St Vincent's Hospital, Fitzroy, Victoria, 3065, Australia
2National Muscle Centre, Howard Florey Institute, Parkville, Victoria, 3010, Australia
3Stem Cell Biology Laboratory, Peter MacCallum Cancer Institute, East Melbourne, Victoria, 3002, Australia
4Centre for Neurosciences, University of Melbourne, Victoria 3010, Australia

Tài liệu tham khảo

Rando, 2000, Rescue of dystrophin expression in mdx mouse muscle by RNA/DNA oligonucleotides, Proc Natl Acad Sci USA, 97, 5363, 10.1073/pnas.97.10.5363 Kapsa, 2001, In vivo and in vitro correction of the mdx dystrophin gene nonsense mutation by short-fragment homologous replacement, Hum Gene Ther, 12, 629, 10.1089/104303401300057324 Ferrari, 1998, Science, 279, 1528, 10.1126/science.279.5356.1528 Bittner, 1999, Recruitment of bone-marrow-derived cells by skeletal and cardiac muscle in adult dystrophic mdx mice, Anat Embryol (Berlin), 199, 391, 10.1007/s004290050237 Gussoni, 1999, Dystrophin expression in the mdx mouse restored by stem cell transplantation, Nature, 401, 390, 10.1038/43919 Kapsa, 2002, Targeted gene correction in the mdx mouse using short DNA fragments: towards application with bone marrow-derived cells for autologous remodelling of dystrophic muscle, Gene Ther, 9, 695, 10.1038/sj.gt.3301737 Rando, 1994, Primary mouse myoblast purification, characterization, and transplantation for cell-mediated gene therapy, J Cell Biol, 125, 1275, 10.1083/jcb.125.6.1275 Vilquin, 1995, Successful histocompatible myoblast transplantation in dystrophin-deficient mdx mouse despite the production of antibodies against dystrophin, J Cell Biol, 131, 975, 10.1083/jcb.131.4.975 Huard, 1994, High efficiency of muscle regeneration after human myoblast clone transplantation in SCID mice, J Clin Invest, 93, 586, 10.1172/JCI117011 Lee, 2000, Clonal isolation of muscle-derived cells capable of enhancing muscle regeneration and bone healing, J Cell Biol, 150, 1085, 10.1083/jcb.150.5.1085 Torrente, 2001, Intraarterial injection of muscle-derived CD34(+)Sca-1(+) stem cells restores dystrophin in mdx mice, J Cell Biol, 152, 335, 10.1083/jcb.152.2.335 Bertoncello, 1997, Surrogate assays for hematopoietic stem cell activity, 35 Bertoni, 2002, Dystrophin gene repair in mdx muscle precursors in vitro and in vivo mediated by RNA–DNA chimeric oligonucleotides, Hum Gene Ther, 13, 707, 10.1089/104303402317322276 Zuk, 2001, Multilineage cells from human adipose tissue: implications for cell-based therapies, Tissue Eng, 7, 211, 10.1089/107632701300062859 Bower, 1997, The role of growth factors in myoblast transfer therapy, Basic Appl Myol, 7, 177