Bone Marrow Transplantation in Congenital Erythropoietic Porphyria: Sustained Efficacy but Unexpected Liver Dysfunction

Biology of Blood and Marrow Transplantation - Tập 26 - Trang 704-711 - 2020
Caroline Besnard1, Caroline Schmitt2, Louise Galmiche-Rolland3, Dominique Debray4, Monique Fabre3, Thierry Molina3, Laurent Gouya2, Cécile Ged5, Martin Castelle1, Marina Cavazzana6, Elisa Magrin6, Bénédicte Neven1, Despina Moshous1, Stéphane Blanche1, Marie-Louise Frémond1
1Pediatric Immuno-Hematology and Rheumatology Unit, Necker Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris, AP-HP, Paris, France
2French Center of Porphyrias, Louis Mourier Hospital, AP-HP, Colombes and Research Center of Inflammation, UMR1149 INSERM, Université de Paris, Paris, France
3Pathology Department, Necker Enfants Malades Hospital, AP-HP, Paris, France
4Pediatric Hepatology Unit, Necker Enfants Malades Hospital, AP-HP, Paris, France
5Biotherapy of Genetic Diseases, Inflammatory Disorders, and Cancers, U1035 INSERM, Bordeaux University, Bordeaux, France
6Biotherapy Unit, Necker Enfants Malades Hospital, AP-HP, Paris, France

Tài liệu tham khảo

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