Alternative therapies to address the unmet medical needs of patients with phenylketonuria

10.1002/humu.20526

Blau N, 2010, Lancet, 376, 1417, 10.1016/S0140-6736(10)60961-0

10.1542/peds.2009-3584

van Spronsen FJ, 2010, J Inherit Metab Dis, 33, 671, 10.1007/s10545-010-9216-1

Santos-Sierra S, 2012, Hum Mol Genet, 21, 1877, 10.1093/hmg/dds001

Blau N, 2010, Expert Rev Endocrinol Metabol, 5, 483, 10.1586/eem.10.39

Heintz C, 2013, Hum Mutat, 34, 927, 10.1002/humu.22320

Blau N, 2014, Expert Rev Mol Diagn, 14, 655, 10.1586/14737159.2014.923760

Wettstein S, 2014, Eur J Hum Genet

Pey AL, 2007, Am J Hum Genet, 81, 1006, 10.1086/521879

Staudigl M, 2011, Hum Mol Genet, 20, 2628, 10.1093/hmg/ddr165

De Maria R, 2014, Stroke, 45, 2959, 10.1161/STROKEAHA.114.005937

Keil S, 2013, Pediatrics, 131, e1881, 10.1542/peds.2012-3291

Shintaku H, 2014, J Pediatr, 165, 1241, 10.1016/j.jpeds.2014.08.003

Longo N, 2014, Genet Med

Hoskins JA, 1980, Lancet, 1, 392, 10.1016/S0140-6736(80)90944-7

10.1073/pnas.0808421105

Sarkissian CN, 2011, Mol Genet Metab, 104, 249, 10.1016/j.ymgme.2011.06.016

Longo N, 2014, Lancet, 384, 37, 10.1016/S0140-6736(13)61841-3

Yew NS, 2013, Mol Genet Metab, 109, 339, 10.1016/j.ymgme.2013.05.011

Rossi L, 2014, J Control Release, 194, 37, 10.1016/j.jconrel.2014.08.012

Levy HL, 2007, Lancet, 370, 504, 10.1016/S0140-6736(07)61234-3

10.1007/s10545-007-0605-z

10.1002/ajmg.a.32562

10.1016/j.jpeds.2008.11.040

10.1016/j.ymgme.2011.03.020

Douglas TD, 2013, Health Qual Life Outcomes, 11, 218, 10.1186/1477-7525-11-218

Grange DK, 2014, Mol Genet Metab, 112, 9, 10.1016/j.ymgme.2014.02.016