A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease

New England Journal of Medicine - Tập 381 Số 6 - Trang 509-519 - 2019
Elliott Vichinsky1, Carolyn Hoppe2, Kenneth I. Ataga3, Russell E. Ware4, Videlis Nduba5, Amal El‐Beshlawy6,7, Hoda Hassab8, Maureen Achebe9, Salam Alkindi10, R. Clark Brown11, David Diuguid12, Paul Telfer13, Dimitris A. Tsitsikas14, Ashraf Elghandour7, Victor R. Gordeuk15, Julie Kanter16, Miguel R. Abboud17, Joshua Lehrer‐Graiwer2, Margaret Tonda2, Allison Intondi2, Barbara Tong2, Jo Howard18
1Benioff Children’s Hospital Oakland, Oakland
2Global Blood Therapeutics, South San Francisco
3University of Tennessee Health Science Center at Memphis, Memphis
4Cincinnati Children’s Hospital and University of Cincinnati, Cincinnati
5Kenya Medical Research Institute, Kisumu, Kenya
6Cairo University, Cairo
7Faculty of Medicine
8Pediatric Department and Clinical Research Center, Faculty of Medicine
9Brigham and Women’s Hospital and Harvard Medical School, Boston, Alexandria University, Alexandria
10Sultan Qaboos University, Muscat, Oman, Alexandria University, Alexandria
11Emory University and Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Atlanta, Alexandria University, Alexandria
12New York–Presbyterian/Columbia University Medical Center, New York, Alexandria University, Alexandria
13Barts Health NHS Trust, Alexandria University, Alexandria
14Homerton University Hospital NHS Foundation Trust, Alexandria University, Alexandria
15University of Illinois at Chicago, Chicago
16University of Alabama at Birmingham, Birmingham
17American University of Beirut Medical Center, Beirut, Lebanon
18Guy’s and St. Thomas’ NHS Foundation Trust and King’s College, Alexandria University, Alexandria

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New England Journal of Medicine

Tập 381 Số 6

509-519

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