Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice

Molecular Therapy - Methods & Clinical Development - Tập 16 - Trang 78-93 - 2020
Denise A. Carbonaro-Sarracino1, Alice F. Tarantal2,3, C. Chang I. Lee2,3, Michael L. Kaufman1, Stephen Wandro1, Xiangyang Jin1, Michele Martinez2,3, Danielle N. Clark1, Krista Chun1, Colin Koziol1, Cinnamon L. Hardee1, Xiaoyan Wang4, Donald B. Kohn1,5,6
1Department of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, Los Angeles, CA 90095, USA
2Center for Fetal Monkey Gene Transfer for Heart, Lung, and Blood Diseases, University of California, Davis, Davis, CA 95616, USA
3Departments of Pediatrics and Cell Biology and Human Anatomy, School of Medicine, and California National Primate Research Center, University of California, Davis, Davis, CA 95616, USA
4Department of General Internal Medicine and Health Services Research, University of California, Los Angeles, Los Angeles, CA 90095, USA
5Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles, CA 90095, USA
6The Eli & Edythe Broad Center for Stem Cells and Regenerative Medicine, University of California, Los Angeles, Los Angeles, CA 90095, USA

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Molecular Therapy - Methods & Clinical Development

Tập 16

78-93

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