Establishing diagnostic criteria for severe combined immunodeficiency disease (SCID), leaky SCID, and Omenn syndrome: The Primary Immune Deficiency Treatment Consortium experience

Journal of Allergy and Clinical Immunology - Tập 133 Số 4 - Trang 1092-1098 - 2014
William T. Shearer1, Elizabeth Dunn2, Luigi D. Notarangelo3, Christopher C. Dvorak2, Jennifer M. Puck2, Brent R. Logan4, Linda M. Griffith5, Donald B. Kohn6, Richard J. O’Reilly7, Thomas A. Fleisher8, Sung‐Yun Pai9, Caridad Martinez10, Rebecca H. Buckley11, Morton J. Cowan2
1Department of Pediatrics, Section of Immunology, Allergy, and Rheumatology, Baylor College of Medicine, Texas Children's Hospital, Houston, Tex
2Division of Pediatric Allergy, Immunology, and Blood and Marrow Transplant, Benioff Children's Hospital, University of California San Francisco, San Francisco, Calif
3Division of Biostatistics, Center for International Blood and Marrow Transplant Research, Medical College of Wisconsin, Milwaukee, Wis
4Division of Immunology and the Manton Center for Orphan Disease Research, Children's Hospital Boston, and Harvard Stem Cell Institute, Harvard Medical School, Boston, Mass
5Division of Allergy, Immunology and Transplantation, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, Md
6Departments of Microbiology, Immunology & Molecular Genetics and Pediatrics, University of California, Los Angeles, Calif.
7Department of Pediatrics, Memorial Sloan Kettering Cancer Center, New York, NY
8Department of Laboratory Medicine, Clinical Center, National Institutes of Health, Bethesda, MD
9Division of Hematology and Oncology, Boston Children's Hospital, and Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Mass
10Center for Cell and Gene Therapy, Baylor College of Medicine, Texas Children's Hospital Cancer Center, Houston, Tex
11Department of Pediatrics and Immunology, Duke University Medical Center, Durham, NC;

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Journal of Allergy and Clinical Immunology

Tập 133 Số 4

1092-1098

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