Tocilizumab treatment in childhood Takayasu arteritis: Case series of four patients and systematic review of the literature

Seminars in Arthritis and Rheumatism - Tập 46 - Trang 529-535 - 2017
Ezgi Deniz Batu1, Hafize Emine Sönmez1, Tuncay Hazırolan2, Fatih Özaltın3, Yelda Bilginer1, Seza Özen1
1Division of Rheumatology, Department of Pediatrics, Hacettepe University Faculty of Medicine, Ankara 06100, Turkey
2Department of Radiology, Hacettepe University Faculty of Medicine, Ankara, Turkey
3Division of Nephrology, Department of Pediatrics, Hacettepe University Faculty of Medicine, Ankara, Turkey

Tài liệu tham khảo

Jennette, 2013, 2012 revised International Chapel Hill Consensus Conference Nomenclature of Vasculitides, Arthritis Rheum, 65, 1, 10.1002/art.37715 Fries, 1990, The American College of Rheumatology 1990 criteria for the classification of vasculitis. Summary, Arthritis Rheum, 33, 1135, 10.1002/art.1780330812 Jain, 2000, Takayasu arteritis in children and young indians, Int J Cardiol, 75, S153, 10.1016/S0167-5273(00)00180-7 Arend, 1990, The American College of Rheumatology 1990 criteria for the classification of Takayasu arteritis, Arthritis Rheum, 33, 1129, 10.1002/art.1780330811 Kerr, 1994, Takayasu arteritis, Ann Int Med, 120, 919, 10.7326/0003-4819-120-11-199406010-00004 Singh, 2013, Takayasu arteritis in infancy, Rheumatology (Oxford), 52, 2093, 10.1093/rheumatology/ket109 Ozen, 2007, Childhood vasculitides in Turkey: a nationwide survey, Clin Rheumatol, 26, 196 Unizony, 2013, New treatment strategies in large-vessel vasculitis, Curr Opin Rheumatol, 25, 3, 10.1097/BOR.0b013e32835b133a Misra, 2013, Development and initial validation of the Indian Takayasu Clinical Activity Score (ITAS2010), Rheumatology (Oxford), 52, 1795, 10.1093/rheumatology/ket128 Arnaud, 2011, Pathogenesis of Takayasu’s arteritis: a 2011 update, Autoimmun Rev, 11, 61, 10.1016/j.autrev.2011.08.001 Park, 2006, Serum cytokine profiles and their correlations with disease activity in Takayasu’s arteritis, Rheumatology (Oxford), 45, 545, 10.1093/rheumatology/kei266 Nishimoto, 2006, Interleukin 6: from bench to bedside, Nat Clin Pract Rheumatol, 2, 619, 10.1038/ncprheum0338 Tombetti, 2014, Anti-cytokine treatment for Takayasu arteritis: state of the art, Intractable Rare Dis Res, 3, 29, 10.5582/irdr.3.29 Arnaud, 2010, Takayasu arteritis in France: a single-center retrospective study of 82 cases comparing white, North African, and Black patients, Medicine (Baltimore), 89, 1, 10.1097/MD.0b013e3181cba0a3 Tombetti, 2013, Treatment of refractory Takayasu arteritis with tocilizumab: 7 Italian patients from a single referral center, J Rheumatol, 40, 2047, 10.3899/jrheum.130536 Ozen, 2007, Takayasu arteritis in children: preliminary experience with cyclophosphamide induction and corticosteroids followed by methotrexate, J Pediatr, 150, 72, 10.1016/j.jpeds.2006.10.059 Abisror, 2013, Tocilizumab in refractory Takayasu arteritis: a case series and updated literature review, Autoimmun Rev, 12, 1143, 10.1016/j.autrev.2013.06.019 Nakaoka, 2013, Tocilizumab for the treatment of patients with refractory Takayasu arteritis, Int Heart J, 54, 405, 10.1536/ihj.54.405 Osman, 2015, Tocilizumab for treating Takayasu’s arteritis and associated stroke: a case series and updated review of the literature, J Stroke Cerebrovasc Dis, 24, 1291, 10.1016/j.jstrokecerebrovasdis.2015.01.032 Ozen, 2010, EULAR/PRINTO/PRES criteria for Henoch–Schonlein purpura, childhood polyarteritis nodosa, childhood Wegener granulomatosis and childhood Takayasu arteritis: Ankara 2008. Part II: final classification criteria, Ann Rheum Dis, 69, 798, 10.1136/ard.2009.116657 Bravo Mancheno, 2012, Successful tocilizumab treatment in a child with refractory Takayasu arteritis, Pediatrics, 130, e1720, 10.1542/peds.2012-1384 Bredemeier, 2012, One-year clinical and radiological evolution of a patient with refractory Takayasu′s arteritis under treatment with tocilizumab, Clin Exp Rheumatol, 30, S98 Canas, 2014, Efficacy and safety of anti-interleukin 6 receptor monoclonal antibody (tocilizumab) in Colombian patients with Takayasu arteritis, J Clin Rheumatol, 20, 125, 10.1097/RHU.0000000000000098 de Kruif, 2012, Streptococcal lung abscesses from a dental focus following tocilizumab: a case report, Clin Exp Rheumatol, 30, 951 Goel, 2013, Rapid control of disease activity by tocilizumab in 10 ‘difficult-to-treat’ cases of Takayasu arteritis, Int J Rheum Dis, 16, 754, 10.1111/1756-185X.12220 Loricera, 2014, Tocilizumab in refractory aortitis: study on 16 patients and literature review, Clin Exp Rheumatol, 32, S79 Mekinian, 2015, Efficacy of biological-targeted treatments in Takayasu arteritis: multicenter, retrospective study of 49 patients, Circulation, 132, 1693, 10.1161/CIRCULATIONAHA.114.014321 Nishimoto, 2008, Successful treatment of a patient with Takayasu arteritis using a humanized anti-interleukin-6 receptor antibody, Arthritis Rheum, 58, 1197, 10.1002/art.23373 Salvarani, 2012, Tocilizumab: a novel therapy for patients with large-vessel vasculitis, Rheumatology (Oxford), 51, 151, 10.1093/rheumatology/ker296 Salvarani, 2012, Rescue treatment with tocilizumab for Takayasu arteritis resistant to TNF-alpha blockers, Clin Exp Rheumatol, 30, S90 Schiavon, 2014, Takayasu arteritis and NYHA III/IV idiopathic cardiomiopathy: tocilizumab proves effective and safe, Joint Bone Spine, 81, 278, 10.1016/j.jbspin.2013.11.008 Seitz, 2011, Rapid induction of remission in large vessel vasculitis by IL-6 blockade. A case series, Swiss Med Wkly, 141, w13156 Unizony, 2012, Tocilizumab for the treatment of large-vessel vasculitis (giant cell arteritis, Takayasu arteritis) and polymyalgia rheumatica, Arthritis Care Res, 64, 1720, 10.1002/acr.21750 Xenitidis, 2013, Sustained inflammation of the aortic wall despite tocilizumab treatment in two cases of Takayasu arteritis, Rheumatology (Oxford), 52, 1729, 10.1093/rheumatology/ket107 Youngstein, 2014, Serial analysis of clinical and imaging indices reveals prolonged efficacy of TNF-alpha and IL-6 receptor targeted therapies in refractory Takayasu arteritis, Clin Exp Rheumatol, 32, S11 Clifford, 2014, Recent advances in the medical management of Takayasu arteritis: an update on use of biologic therapies, Curr Opin Rheumatol, 26, 7, 10.1097/BOR.0000000000000004 Osman, 2014, The role of biological agents in the management of large vessel vasculitis (LVV): a systematic review and meta-analysis, PloS One, 9, e115026, 10.1371/journal.pone.0115026 Arita, 2015, Cytokine storm after cessation of tocilizumab in a patient with refractory Takayasu arteritis, Int J Cardiol, 187, 319, 10.1016/j.ijcard.2015.03.399 Dagna, 2011, Pentraxin-3 as a marker of disease activity in Takayasu arteritis, Ann Int Med, 155, 425, 10.7326/0003-4819-155-7-201110040-00005 Matsuyama, 2003, Matrix metalloproteinases as novel disease markers in Takayasu arteritis, Circulation, 108, 1469, 10.1161/01.CIR.0000090689.69973.B1 Noguchi, 1998, Increased levels of soluble forms of adhesion molecules in Takayasu arteritis, Int J Cardiol, 66, S23, 10.1016/S0167-5273(98)00145-4 Noris, 1999, Interleukin-6 and RANTES in Takayasu arteritis: a guide for therapeutic decisions?, Circulation, 100, 55, 10.1161/01.CIR.100.1.55 Aydin, 2015, Outcome measures for Takayasu’s arteritis, Curr Opin Rheumatol, 27, 32, 10.1097/BOR.0000000000000129 Brunner, 2010, Takayasu arteritis in children and adolescents, Rheumatology (Oxford), 49, 1806, 10.1093/rheumatology/keq167 Cakar, 2008, Takayasu arteritis in children, J Rheumatol, 35, 913 Eleftheriou, 2015, Vasculitis in children, Nephrol Dial Transplant, 30, i94 Morales, 1991, Takayasu’s arteritis in children, J Rheumatol, 18, 1081 Park, 2005, Clinical characteristics and outcomes of Takayasu’s arteritis: analysis of 108 patients using standardized criteria for diagnosis, activity assessment, and angiographic classification, Scand J Rheumatol, 34, 284, 10.1080/03009740510026526